Administration practices of and adherence to nusinersen in children with spinal muscular atrophy: a multicenter disease registry study in China
中国多中心疾病登记研究:儿童脊髓性肌萎缩症患者诺西那生治疗的管理实践及依从性
期刊:BMC Pediatrics
影响因子:2
doi:10.1186/s12887-024-05290-0
Peng, Jing; Yao, Xiaoli; Luo, Rong; Wang, Xiuxia; Wu, Liwen; Zhong, Jianmin; Jin, Ruifeng; Lu, Xinguo; Liang, Jianmin; Hong, Siqi; Yang, Lin; Zhang, Xiaoli; Mao, Shanshan; Tao, Zhe; Hu, Jun; Sun, Dan; Wang, Hua; Zhang, Li; Xia, Yanyan; Chen, Ken; Wang, Yi