The use of sodium DL-3-Hydroxybutyrate in severe acute neuro-metabolic compromise in patients with inherited ketone body synthetic disorders
在患有遗传性酮体合成障碍的患者中,DL-3-羟基丁酸钠可用于治疗严重的急性神经代谢障碍。
期刊:Orphanet Journal of Rare Diseases
影响因子:3.5
doi:10.1186/s13023-020-1316-x
Bhattacharya, Kaustuv; Matar, Walid; Tolun, Adviye Ayper; Devanapalli, Beena; Thompson, Sue; Dalkeith, Troy; Lichkus, Kate; Tchan, Michel