日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

AAV-delivered PPT1 provides long-term neurological benefits in CLN1 mice and achieves therapeutic levels in sheep brain

AAV递送的PPT1在CLN1小鼠中可提供长期的神经系统获益,并在绵羊脑中达到治疗水平。

Alam, Md Suhail; Khatiwada, Apeksha; Eaton, Samantha L; Cohen, Daniel M; White, John; Derby, Melissa; Peterson, Drew; Rivera-Pena, Graciela; Nayal, Mohamad; Becker, Mallory; Beck, Heena; Li, Charlie; Gentzel, Renee; Atkins, George; Greenhalgh, Stephen N; Lillico, Simon G; Gregson, Rachael; Clutton, Eddie; Murdoch, Fraser; Nixon, James; Gray, Mark; Thompson, Gerard; McBride, Jodi; Wishart, Thomas M; Biferi, Maria Grazia; Ramsburg, Elizabeth

GARP and EARP are required for efficient BoHV-1 replication as identified by a genome wide CRISPR knockout screen

全基因组 CRISPR 敲除筛选结果表明,GARP 和 EARP 是 BoHV-1 有效复制所必需的。

Tan, Wenfang S; Rong, Enguang; Dry, Inga; Lillico, Simon G; Law, Andy; Digard, Paul; Whitelaw, Bruce; Dalziel, Robert G

Cross-species efficacy of enzyme replacement therapy for CLN1 disease in mice and sheep

酶替代疗法治疗小鼠和绵羊CLN1疾病的跨物种疗效

Nelvagal, Hemanth R; Eaton, Samantha L; Wang, Sophie H; Eultgen, Elizabeth M; Takahashi, Keigo; Le, Steven Q; Nesbitt, Rachel; Dearborn, Joshua T; Siano, Nicholas; Puhl, Ana C; Dickson, Patricia I; Thompson, Gerard; Murdoch, Fraser; Brennan, Paul M; Gray, Mark; Greenhalgh, Stephen N; Tennant, Peter; Gregson, Rachael; Clutton, Eddie; Nixon, James; Proudfoot, Chris; Guido, Stefano; Lillico, Simon G; Whitelaw, C Bruce A; Lu, Jui-Yun; Hofmann, Sandra L; Ekins, Sean; Sands, Mark S; Wishart, Thomas M; Cooper, Jonathan D

Modelling Neurological Diseases in Large Animals: Criteria for Model Selection and Clinical Assessment

大型动物神经系统疾病建模:模型选择和临床评估标准

Eaton, Samantha L; Murdoch, Fraser; Rzechorzek, Nina M; Thompson, Gerard; Hartley, Claudia; Blacklock, Benjamin Thomas; Proudfoot, Chris; Lillico, Simon G; Tennant, Peter; Ritchie, Adrian; Nixon, James; Brennan, Paul M; Guido, Stefano; Mitchell, Nadia L; Palmer, David N; Whitelaw, C Bruce A; Cooper, Jonathan D; Wishart, Thomas M

Erratum for Burkard et al., "Pigs Lacking the Scavenger Receptor Cysteine-Rich Domain 5 of CD163 Are Resistant to Porcine Reproductive and Respiratory Syndrome Virus 1 Infection"

Burkard 等人的论文“缺乏 CD163 清道夫受体富含半胱氨酸结构域 5 的猪对猪繁殖与呼吸综合征病毒 1 型感染具有抵抗力”的勘误

Burkard, Christine; Opriessnig, Tanja; Mileham, Alan J; Stadejek, Tomasz; Ait-Ali, Tahar; Lillico, Simon G; Whitelaw, C Bruce A; Archibald, Alan L

Generation of germline ablated male pigs by CRISPR/Cas9 editing of the NANOS2 gene

利用CRISPR/Cas9技术编辑NANOS2基因,生成生殖系消融的雄性猪

Park, Ki-Eun; Kaucher, Amy V; Powell, Anne; Waqas, Muhammad Salman; Sandmaier, Shelley E S; Oatley, Melissa J; Park, Chi-Hun; Tibary, Ahmed; Donovan, David M; Blomberg, Le Ann; Lillico, Simon G; Whitelaw, C Bruce A; Mileham, Alan; Telugu, Bhanu P; Oatley, Jon M

Engineering large animal models of human disease

构建人类疾病的大型动物模型

Whitelaw, C Bruce A; Sheets, Timothy P; Lillico, Simon G; Telugu, Bhanu P

Comparison of CRISPR/Cas9 and TALENs on editing an integrated EGFP gene in the genome of HEK293FT cells

比较 CRISPR/Cas9 和 TALENs 在 HEK293FT 细胞基因组中编辑整合的 EGFP 基因的效果

He, Zuyong; Proudfoot, Chris; Whitelaw, C Bruce A; Lillico, Simon G

Live pigs produced from genome edited zygotes

由基因编辑受精卵培育出的活猪

Lillico, Simon G; Proudfoot, Chris; Carlson, Daniel F; Stverakova, Dana; Neil, Claire; Blain, Carol; King, Tim J; Ritchie, William A; Tan, Wenfang; Mileham, Alan J; McLaren, David G; Fahrenkrug, Scott C; Whitelaw, C Bruce A

Stable conditional expression and effect of C/ebpβ-LIP in adipocytes using the pSLIK system.

利用 pSLIK 系统在脂肪细胞中稳定条件表达 C/ebpβ-LIP 及其作用

Esteves Cristina L, Kelly Val, Bégay Valérie, Lillico Simon G, Leutz Achim, Seckl Jonathan R, Chapman Karen E