日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

SAT-628 Navigating through the Challenges of Autoimmune Polyendocrine Syndromes

SAT-628 应对自身免疫性多内分泌综合征的挑战

Laursen, Nick S; Friesen, Robert H E; Zhu, Xueyong; Jongeneelen, Mandy; Blokland, Sven; Vermond, Jan; van Eijgen, Alida; Tang, Chan; van Diepen, Harry; Obmolova, Galina; van der Neut Kolfschoten, Marijn; Zuijdgeest, David; Straetemans, Roel; Hoffman, Ryan M B; Nieusma, Travis; Pallesen, Jesper; Turner, Hannah L; Bernard, Steffen M; Ward, Andrew B; Luo, Jinquan; Poon, Leo L M; Tretiakova, Anna P; Wilson, James M; Limberis, Maria P; Vogels, Ronald; Brandenburg, Boerries; Kolkman, Joost A; Wilson, Ian A; Akhter, Wajeeha; Azmat, Shazia; Akhter, Rimsha; Zaidi, Aniqa J; Gilden, Janice L

Durable transgene expression and efficient re-administration after rAAV2.5T-mediated fCFTRΔR gene delivery to adult ferret lungs

rAAV2.5T介导的fCFTRΔR基因递送至成年雪貂肺部后,转基因表达持久且可有效重复给药

Tang, Yinghua; Ebadi, Mehrnoosh; Lei, Junying; Feng, Zehua; Fakhari, Shahab; Wu, Peipei; Smith, Mark D; Limberis, Maria P; Kolbeck, Roland; Excoffon, Katherine J; Yan, Ziying; Engelhardt, John F

Gene Therapeutics for Surfactant Dysfunction Disorders: Targeting the Alveolar Type 2 Epithelial Cell

针对肺表面活性物质功能障碍疾病的基因疗法:靶向肺泡II型上皮细胞

Sitaraman, Sneha; Alysandratos, Konstantinos-Dionysios; Wambach, Jennifer A; Limberis, Maria P

Non-Clinical Study Examining AAV8.TBG.hLDLR Vector-Associated Toxicity in Chow-Fed Wild-Type and LDLR(+/-) Rhesus Macaques

非临床研究:检测AAV8.TBG.hLDLR载体对饲喂普通饲料的野生型和LDLR(+/-)恒河猴的毒性

Greig, Jenny A; Limberis, Maria P; Bell, Peter; Chen, Shu-Jen; Calcedo, Roberto; Rader, Daniel J; Wilson, James M

Nonclinical Pharmacology/Toxicology Study of AAV8.TBG.mLDLR and AAV8.TBG.hLDLR in a Mouse Model of Homozygous Familial Hypercholesterolemia

在纯合子家族性高胆固醇血症小鼠模型中,AAV8.TBG.mLDLR 和 AAV8.TBG.hLDLR 的非临床药理学/毒理学研究

Greig, Jenny A; Limberis, Maria P; Bell, Peter; Chen, Shu-Jen; Calcedo, Roberto; Rader, Daniel J; Wilson, James M

Vector serotype screening for use in ovine perinatal lung gene therapy

用于绵羊围产期肺基因治疗的载体血清型筛选

McClain, Lauren E; Davey, Marcus G; Zoltick, Phillip W; Limberis, Maria P; Flake, Alan W; Peranteau, William H

Developmental stage determines efficiency of gene transfer to muscle satellite cells by in utero delivery of adeno-associated virus vector serotype 2/9.

发育阶段决定了通过子宫内递送腺相关病毒载体 2/9 型将基因转移到肌肉卫星细胞的效率

Stitelman David H, Brazelton Tim, Bora Archana, Traas Jeremy, Merianos Demetri, Limberis Maria, Davey Marcus, Flake Alan W

In vivo evaluation of adeno-associated virus gene transfer in airways of mice with acute or chronic respiratory infection

在患有急性或慢性呼吸道感染的小鼠气道中对腺相关病毒基因转移进行体内评估

Myint, Melissa; Limberis, Maria P; Bell, Peter; Somanathan, Suryanarayan; Haczku, Angela; Wilson, James M; Diamond, Scott L

Adeno-associated virus 9-mediated airway expression of antibody protects old and immunodeficient mice against influenza virus

腺相关病毒9介导的气道抗体表达可保护老年和免疫缺陷小鼠免受流感病毒感染

Adam, Virginie S; Crosariol, Marco; Kumar, Sachin; Ge, Moyar Q; Czack, Sarah E; Roy, Soumitra; Haczku, Angela; Tretiakova, Anna; Wilson, James M; Limberis, Maria P

Low sphingosine-1-phosphate impairs lung dendritic cells in cystic fibrosis

囊性纤维化患者肺树突状细胞功能受损,表现为鞘氨醇-1-磷酸水平低下

Xu, Yaqin; Krause, Anja; Limberis, Maria; Worgall, Tilla S; Worgall, Stefan