Rescue of hearing by adenine base editing in a humanized mouse model of Usher syndrome type 1F
通过腺嘌呤碱基编辑挽救 1F 型 Usher 综合征人源化小鼠模型的听力
期刊:Molecular Therapy
影响因子:12.1
doi:10.1016/j.ymthe.2023.06.007
Cole W Peters, Killian S Hanlon, Maryna V Ivanchenko, Eric Zinn, Elizabeth F Linarte, Yaqiao Li, Jonathan M Levy, David R Liu, Benjamin P Kleinstiver, Artur A Indzhykulian, David P Corey