Intracerebroventricular dosing of N-sulfoglucosamine sulfohydrolase in mucopolysaccharidosis IIIA mice reduces markers of brain lysosomal dysfunction
在粘多糖贮积症 IIIA 小鼠脑室内注射 N-磺基葡萄糖胺磺基水解酶可降低脑溶酶体功能障碍标志物
期刊:Journal of Biological Chemistry
影响因子:4
doi:10.1016/j.jbc.2022.102625
Jenna Magat, Samantha Jones, Brian Baridon, Vishal Agrawal, Hio Wong, Alexander Giaramita, Linley Mangini, Britta Handyside, Catherine Vitelli, Monica Parker, Natasha Yeung, Yu Zhou, Erno Pungor, Ilya Slabodkin, Olivia Gorostiza, Allora Aguilera, Melanie J Lo, Saida Alcozie, Terri M Christianson, Pa