Personalized CFTR Modulator Therapy for G85E and N1303K Homozygous Patients with Cystic Fibrosis
针对 G85E 和 N1303K 纯合囊性纤维化患者的个性化 CFTR 调节剂治疗
期刊:International Journal of Molecular Sciences
影响因子:0.7
doi:10.3390/ijms241512365
Simon Y Graeber, Anita Balázs, Niklas Ziegahn, Tihomir Rubil, Constanze Vitzthum, Linus Piehler, Marika Drescher, Kathrin Seidel, Alexander Rohrbach, Jobst Röhmel, Stephanie Thee, Julia Duerr, Marcus A Mall, Mirjam Stahl