Measuring the effect of newborn screening on survival after haematopoietic cell transplantation for severe combined immunodeficiency: a 36-year longitudinal study from the Primary Immune Deficiency Treatment Consortium
衡量新生儿筛查对重症联合免疫缺陷造血干细胞移植后生存率的影响:来自原发性免疫缺陷治疗联盟的一项为期36年的纵向研究
期刊:Lancet
影响因子:88.5
doi:10.1016/S0140-6736(23)00731-6
Thakar, Monica S; Logan, Brent R; Puck, Jennifer M; Dunn, Elizabeth A; Buckley, Rebecca H; Cowan, Morton J; O'Reilly, Richard J; Kapoor, Neena; Satter, Lisa Forbes; Pai, Sung-Yun; Heimall, Jennifer; Chandra, Sharat; Ebens, Christen L; Chellapandian, Deepak; Williams, Olatundun; Burroughs, Lauri M; Saldana, Blachy Davila; Rayes, Ahmad; Madden, Lisa M; Chandrakasan, Shanmuganathan; Bednarski, Jeffrey J 2nd; DeSantes, Kenneth B; Cuvelier, Geoffrey D E; Teira, Pierre; Gillio, Alfred P; Eissa, Hesham; Knutsen, Alan P; Goldman, Frederick D; Aquino, Victor M; Shereck, Evan B; Moore, Theodore B; Caywood, Emi H; Lugt, Mark T Vander; Rozmus, Jacob; Broglie, Larisa; Yu, Lolie C; Shah, Ami J; Andolina, Jeffrey R; Liu, Xuerong; Parrott, Roberta E; Dara, Jasmeen; Prockop, Susan; Martinez, Caridad A; Kapadia, Malika; Jyonouchi, Soma C; Sullivan, Kathleen E; Bleesing, Jack J; Chaudhury, Sonali; Petrovic, Aleksandra; Keller, Michael D; Quigg, Troy C; Parikh, Suhag; Shenoy, Shalini; Seroogy, Christine; Rubin, Tamar; Decaluwe, Hélène; Routes, John M; Torgerson, Troy R; Leiding, Jennifer W; Pulsipher, Michael A; Kohn, Donald B; Griffith, Linda M; Haddad, Elie; Dvorak, Christopher C; Notarangelo, Luigi D