日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Hematopoietic cell transplantation for Wiskott-Aldrich syndrome: a PIDTC report

造血干细胞移植治疗威斯科特-奥尔德里奇综合征:PIDTC报告

Alexander, Jessie L; Dávila Saldaña, Blachy J; Brazauskas, Ruta; Dammalapati, Sravya Gethika; Griffith, Linda M; Shah, Ami J; Shimano, Kristin A; Ochs, Hans D; Bleesing, Jack J; Ebens, Christen L; Kapadia, Malika; Bauchat, Andrea; Kapoor, Neena; Oved, Joseph H; Eissa, Hesham; Lust, Hannah; Keller, Michael D; Haines, Hilary; Chandrakasan, Shanmuganathan; Talano, Julie-An; Rayes, Ahmad; Madden, Lisa; Shereck, Evan; Miller, Holly K; Satter, Lisa Forbes; Martinez, Caridad; Rozmus, Jacob; Bednarski, Jeffrey J; Yu, Lolie C; Chellapandian, Deepakbabu; Aquino, Victor M; Knutsen, Alan; Chong, Hey; Chopek, Ashley; Gillio, Alfred P; Joshi, Avni; Rangarajan, Hemalatha; Moore, Theodore B; Andolina, Jeffrey R; DeSantes, Kenneth B; Vander Lugt, Mark; Prockop, Susan E; Shyr, David C; Sullivan, Kathleen E; Parikh, Suhag; Weinacht, Katja G; Torgerson, Troy R; Marsh, Rebecca; Dvorak, Christopher C; Chan, Alice Y; Haddad, Elie; Heimall, Jennifer R; Pulsipher, Michael A; Leiding, Jennifer W; Kohn, Donald B; Puck, Jennifer M; Notarangelo, Luigi D; Rawlings, David J; Cowan, Morton J; Petrovic, Aleksandra; Pai, Sung-Yun; Burroughs, Lauri M

Neurodevelopmental outcomes following hematopoietic cell transplantation for patients with severe combined immunodeficiency (SCID): A PIDTC study

造血干细胞移植治疗重症联合免疫缺陷(SCID)患者的神经发育结局:一项PIDTC研究

Brumm, Virdette L; Kidd, Sharon A; Logan, Brent R; Chunara, Farheen; Heimall, Jennifer; Griffith, Linda M; Kohn, Donald B; Sanchez, Lauren; Bednarski, Jeffrey J; Martinez, Caridad; Lugt, Mark Vander; Kapoor, Neena; Wright, Nicola; Spitzer, Barbara; Oved, Joseph H; Chandra, Sharat; Chellapandian, Deepak; Ebens, Christen L; Petrovic, Aleks; Rayes, Ahmad; Haines, Hilary L; Lust, Hannah; Schofield, Hannah-Lise Tirado; Christopher, Lauren; Harris, Lynnette L; Satter, Lisa Forbes; Burroughs, Lauri; Dvorak, Christopher C; Haddad, Elie; Leiding, Jennifer W; Marsh, Rebecca A; Notarangelo, Luigi D; Pai, Sung Yun; Pulsipher, Michael A; Puck, Jennifer M; Cowan, Morton J; Shah, Ami J

Multidisciplinary approach to treating complex immune dysregulation disorders: an adaptive model for institutional implementation

针对复杂免疫失调疾病的多学科治疗方法:一种适用于机构实施的适应性模式

Henderson, Lauren A; Abraham, Roshini S; Ahmed, Aisha; Blount, Lindsey; Canna, Scott W; Chaimowitz, Natalia S; Chandrakasan, Shanmuganathan; Coates, Bria; Connelly, James A; Cooper, Megan A; Duncan, Christine N; French, Anthony; Hazen, Melissa; Hermiston, Michelle L; Nolan, Brian; Ray, Anish; Rose, Melissa J; Satter, Lisa Forbes; Schulert, Grant; Tejtel, Sara Kristen Sexson; Vogel, Tiphanie; Walkovich, Kelly; Zinter, Matt S; Behrens, Edward M

MYO5B and the Polygenic Landscape of Very Early-Onset Inflammatory Bowel Disease in an Ethnically Diverse Population

MYO5B基因与不同种族人群中极早发性炎症性肠病的多基因图谱

Watson, Ashleigh; Harris, R Alan; Engevik, Amy C; Oezguen, Numan; Nicholson, Maribeth R; Dooley, Sarah; Stubler, Rachel; Satter, Lisa Forbes; Karam, Lina B; Kellermayer, Richard

[Not Available]

[无法使用]

Buddingh, Emilie Pauline; Slatter, Mary; Becerra, Juan Carlos Aldave; Garcia, Laura Alonso; von Asmuth, Erik; Baris, Safa; de la Calle-Martín, Oscar; Chan, Alice Y; Chan, Su-Wan Bianca; Chandrakasan, Shanmuganathan; Chellapandian, Deepakbabu; Dara, Jasmeen; Farmand, Susan; Fasth, Anders; Satter, Lisa Forbes; Formankova, Renata; Grunebaum, Eyal; Keogh, Steven J; Kiykim, Ayça; Kühl, Jörn-Sven; Laberko, Alexandra; Leahy, Timothy Ronan; Lindemans, Caroline; Martinez, Caridad; Martínez-Martínez, Laura; Mitchell, William Glenn; Morris, Emma; Oved, Joseph H; Polacik, Maria; Rivière, Jacques G; Roifman, Chaim M; Kilic, Sara Sebnem; Sedlacek, Petr; Shah, Ami J; Vong, Linda; Lankester, Arjan C; Albert, Michael H; Neven, Bénédicte; Torgerson, Troy; Leiding, Jennifer; Schuetz, Catharina; Crisan, Diana; Wortsman, Ximena; Alfageme, Fernando; Scharffetter‐Kochanek, Karin; Crisan, Maria; Bernhard, Lukas; Tarnowietzki, Evelyne; Schneider, Lars Alexander; Schmid‐Wendtner, Monika‐H

Relevance of lymphocyte proliferation to PHA in severe combined immunodeficiency (SCID) and T cell lymphopenia

淋巴细胞增殖与严重联合免疫缺陷(SCID)和T细胞淋巴细胞减少症中植物血凝素(PHA)的相关性

Abraham, Roshini S; Basu, Amrita; Heimall, Jennifer R; Dunn, Elizabeth; Yip, Alison; Kapadia, Malika; Kapoor, Neena; Satter, Lisa Forbes; Buckley, Rebecca; O'Reilly, Richard; Cuvelier, Geoffrey D E; Chandra, Sharat; Bednarski, Jeffrey; Chaudhury, Sonali; Moore, Theodore B; Haines, Hilary; Dávila Saldaña, Blachy J; Chellapandian, Deepakbabu; Rayes, Ahmad; Chen, Karin; Caywood, Emi; Chandrakasan, Shanmuganathan; Lugt, Mark Thomas Vander; Ebens, Christen; Teira, Pierre; Shereck, Evan; Miller, Holly; Aquino, Victor; Eissa, Hesham; Yu, Lolie C; Gillio, Alfred; Madden, Lisa; Knutsen, Alan; Shah, Ami J; DeSantes, Kenneth; Barnum, Jessie; Broglie, Larisa; Joshi, Avni Y; Kleiner, Gary; Dara, Jasmeen; Prockop, Susan; Martinez, Caridad; Mousallem, Talal; Oved, Joseph; Burroughs, Lauri; Marsh, Rebecca; Torgerson, Troy R; Leiding, Jennifer W; Pai, Sung Yun; Kohn, Donald B; Pulsipher, Michael A; Griffith, Linda M; Notarangelo, Luigi D; Cowan, Morton J; Puck, Jennifer; Dvorak, Christopher C; Haddad, Elie

Measuring the effect of newborn screening on survival after haematopoietic cell transplantation for severe combined immunodeficiency: a 36-year longitudinal study from the Primary Immune Deficiency Treatment Consortium

衡量新生儿筛查对重症联合免疫缺陷造血干细胞移植后生存率的影响:来自原发性免疫缺陷治疗联盟的一项为期36年的纵向研究

Thakar, Monica S; Logan, Brent R; Puck, Jennifer M; Dunn, Elizabeth A; Buckley, Rebecca H; Cowan, Morton J; O'Reilly, Richard J; Kapoor, Neena; Satter, Lisa Forbes; Pai, Sung-Yun; Heimall, Jennifer; Chandra, Sharat; Ebens, Christen L; Chellapandian, Deepak; Williams, Olatundun; Burroughs, Lauri M; Saldana, Blachy Davila; Rayes, Ahmad; Madden, Lisa M; Chandrakasan, Shanmuganathan; Bednarski, Jeffrey J 2nd; DeSantes, Kenneth B; Cuvelier, Geoffrey D E; Teira, Pierre; Gillio, Alfred P; Eissa, Hesham; Knutsen, Alan P; Goldman, Frederick D; Aquino, Victor M; Shereck, Evan B; Moore, Theodore B; Caywood, Emi H; Lugt, Mark T Vander; Rozmus, Jacob; Broglie, Larisa; Yu, Lolie C; Shah, Ami J; Andolina, Jeffrey R; Liu, Xuerong; Parrott, Roberta E; Dara, Jasmeen; Prockop, Susan; Martinez, Caridad A; Kapadia, Malika; Jyonouchi, Soma C; Sullivan, Kathleen E; Bleesing, Jack J; Chaudhury, Sonali; Petrovic, Aleksandra; Keller, Michael D; Quigg, Troy C; Parikh, Suhag; Shenoy, Shalini; Seroogy, Christine; Rubin, Tamar; Decaluwe, Hélène; Routes, John M; Torgerson, Troy R; Leiding, Jennifer W; Pulsipher, Michael A; Kohn, Donald B; Griffith, Linda M; Haddad, Elie; Dvorak, Christopher C; Notarangelo, Luigi D

The diagnosis of severe combined immunodeficiency: Implementation of the PIDTC 2022 Definitions

重症联合免疫缺陷的诊断:PIDTC 2022 定义的实施

Dvorak, Christopher C; Haddad, Elie; Heimall, Jennifer; Dunn, Elizabeth; Cowan, Morton J; Pai, Sung-Yun; Kapoor, Neena; Satter, Lisa Forbes; Buckley, Rebecca H; O'Reilly, Richard J; Chandra, Sharat; Bednarski, Jeffrey J; Williams, Olatundun; Rayes, Ahmad; Moore, Theodore B; Ebens, Christen L; Davila Saldana, Blachy J; Petrovic, Aleksandra; Chellapandian, Deepak; Cuvelier, Geoffrey D E; Vander Lugt, Mark T; Caywood, Emi H; Chandrakasan, Shanmuganathan; Eissa, Hesham; Goldman, Frederick D; Shereck, Evan; Aquino, Victor M; Desantes, Kenneth B; Madden, Lisa M; Miller, Holly K; Yu, Lolie; Broglie, Larisa; Gillio, Alfred; Shah, Ami J; Knutsen, Alan P; Andolina, Jeffrey P; Joshi, Avni Y; Szabolcs, Paul; Kapadia, Malika; Martinez, Caridad A; Parrot, Roberta E; Sullivan, Kathleen E; Prockop, Susan E; Abraham, Roshini S; Thakar, Monica S; Leiding, Jennifer W; Kohn, Donald B; Pulsipher, Michael A; Griffith, Linda M; Notarangelo, Luigi D; Puck, Jennifer M

The diagnosis of severe combined immunodeficiency (SCID): The Primary Immune Deficiency Treatment Consortium (PIDTC) 2022 Definitions

重症联合免疫缺陷病 (SCID) 的诊断:原发性免疫缺陷治疗联盟 (PIDTC) 2022 年定义

Dvorak, Christopher C; Haddad, Elie; Heimall, Jennifer; Dunn, Elizabeth; Buckley, Rebecca H; Kohn, Donald B; Cowan, Morton J; Pai, Sung-Yun; Griffith, Linda M; Cuvelier, Geoffrey D E; Eissa, Hesham; Shah, Ami J; O'Reilly, Richard J; Pulsipher, Michael A; Wright, Nicola A M; Abraham, Roshini S; Satter, Lisa Forbes; Notarangelo, Luigi D; Puck, Jennifer M

546. COVID-19 Monoclonal Antibody Use at a Stand Alone Children’s Hospital

546. 独立儿童医院使用新冠病毒单克隆抗体

Thomson, C A; Wang, Y; Jackson, L M; Olson, M; Wang, W; Liavonchanka, A; Keleta, L; Silva, V; Diederich, S; Jones, R B; Gubbay, J; Pasick, J; Petric, M; Jean, François; Allen, V G; Brown, E G; Rini, J M; Schrader, J W; Stimes, Grant T; Rodriguez, Brittany; Gillispie, Amanda; Hilliard, Tanya J; Munoz, Flor M; Satter, Lisa Forbes