日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Renovating Neural Networks With Viral-Mediated Gene Transfer From A Tissue Contacting Matrix Mimic

利用病毒介导的基因转移从组织接触基质模拟物中改造神经网络

Dehnavi, Shiva Soltani; Mahmoudi, Negar; Wang, Yi; Cheeseman, Samuel; Ferreira, Rita; Hannan, Ross D; Lisowski, Leszek; Craig, Vincent S J; Moriarty, Niamh; Parish, Clare L; Williams, Richard J; Nisbet, David R

High-throughput evaluation of cardiac-specific promoters for adeno-associated virus mediated cardiac gene therapy

利用高通量方法评估腺相关病毒介导的心脏基因治疗中心脏特异性启动子

Ravindran, Dhanya; Rao, Renuka; Mundisugih, Juan; Titus, Tracy; Tsurusaki, Shinya; Kok, Cindy Y; Rashid, Fairooj N; Igoor, Sindhu; Kotake, Yasuhito; Kumar, Saurabh; Chong, James J H; Alexander, Ian E; Lisowski, Leszek; Kizana, Eddy

Impact of liver fibrosis on AAV-mediated gene transfer to mouse hepatocytes

肝纤维化对AAV介导的基因转移至小鼠肝细胞的影响

Ferriero, Rosa; Bruno, Gemma; Padula, Agnese; Pisano, Simone; Boffa, Iolanda; Gargaro, Marco; Imperatore, Teresa; Battipaglia, Maria; Vivenzio, Silvia; Perna, Claudia; Nusco, Edoardo; Ferrante, Luigi; Westhaus, Adrian; Knight, Maddison; Manni, Giorgia; Campione, Severo; Di Napoli, Evaristo; Polishchuk, Elena; Polishchuk, Roman; Paciello, Orlando; Brunetti-Pierri, Nicola; Lisowski, Leszek; Fallarino, Francesca; Piccolo, Pasquale

Tailoring capsid-directed evolution technology for improved AAV-mediated CAR-T generation.

针对衣壳定向进化技术进行改造,以改进AAV介导的CAR-T细胞生成

Westhaus Adrian, Barba-Sarasua Elena, Chen Yuyan, Hsu Kenneth, Scott Suzanne, Knight Maddison, Haase Florencia, Mesa Mora Santiago, Houghton Benjamin C, Roca-Pinilla Ramon, Kalajdzic Predrag, O'Neill Geraldine, Thrasher Adrian J, Santilli Giorgia, Lisowski Leszek

Wild-type and engineered adeno-associated viral vectors produce comparable opsin expression and light-evoked responses in rat skeletal muscle.

野生型和工程化腺相关病毒载体在大鼠骨骼肌中产生相似的视蛋白表达和光诱发反应

Knapman Fiona L, Cohen E Myfanwy, Kulaga Tom, Lovell Nigel H, Lisowski Leszek, Burke Peter G R, Bilston Lynne E

Critical impact of lysine 136 in TDP-43 phase separation, compartmentalization, and aggregation in living vertebrates.

赖氨酸 136 对活脊椎动物中 TDP-43 相分离、区室化和聚集具有关键影响

Maurel Cindy, Scherer Natalie M, Luu Luan, Radford Rowan A, Hogan Alison, Merjane Jessica, Vidal-Itriago Andres, Don Emily K, Chapman Tyler, Cull Stephen, Vourc'h Patrick, Lisowski Leszek, Lee Albert, Chung Roger S, Morsch Marco

Genotypic, functional, and phenotypic characterization in CTNNB1 neurodevelopmental syndrome.

CTNNB1神经发育综合征的基因型、功能和表型特征

Žakelj Nina, Gosar David, Miroševič Špela, Sanders Stephan J, Ljungdahl Alicia, Kohani Sayeh, Huang Shouhe, Leong Lok I, An Ying, Teo Miou-Jing, Moultrie Fiona, Jerala Roman, Lainšček Duško, Forstnerič Vida, Sušjan Petra, Lisowski Leszek, Perez-Iturralde Andrea, Mrak Jasna Oražem, Chan Ho Yin Edwin, Osredkar Damjan

Paving the way toward treatment solutions for CTNNB1 syndrome: a patient organization perspective

为CTNNB1综合征的治疗方案铺平道路:患者组织的视角

Miroševič, Špela; Khandelwal, Shivang; Amerson, Emily; Parks, Effie; Parks, Mariana; Cochran, Lauren; González Hernández, Ana; Ferraro, Mirela; Lisowski, Leszek; Perez-Iturralde, Andrea; Chung, Wendy; Jacob, Michele H; Žakelj, Nina; Lainšček, Duško; Forstnerič, Vida; Sušjan, Petra; Maruna, Matea; Jerala, Roman; Osredkar, Damjan

Maturation of human cardiac organoids enables complex disease modeling and drug discovery

人类心脏类器官的成熟使得复杂疾病建模和药物发现成为可能。

Pocock, Mark W; Reid, Janice D; Robinson, Harley R; Charitakis, Natalie; Krycer, James R; Foster, Simon R; Fitzsimmons, Rebecca L; Lor, Mary; Devilée, Lynn A C; Batho, Christopher A P; Tuano, Natasha; Howden, Sara E; Vlahos, Katerina; Watt, Kevin I; Piers, Adam T; Bibby, Kaitlyn; McNamara, James W; Sutton, Rebecca; Iaprintsev, Valerii; Mathew, Jacob; Voges, Holly K; Fortuna, Patrick R J; Bass-Stringer, Sebastian; Vivien, Celine; Rae, James; Parton, Robert G; Firulli, Anthony B; Lisowski, Leszek; Huckstep, Hannah; Humphrey, Sean J; Lal, Sean; Konstantinov, Igor E; Weintraub, Robert G; Elliott, David A; Ramialison, Mirana; Porrello, Enzo R; Mills, Richard J; Hudson, James E

Characterization of RNA editing and gene therapy with a compact CRISPR-Cas13 in the retina

利用紧凑型 CRISPR-Cas13 在视网膜中进行 RNA 编辑和基因治疗的特性研究

Kumar, Satheesh; Hsiao, Yi-Wen; Wong, Vickie H Y; Aubin, Deborah; Wang, Jiang-Hui; Lisowski, Leszek; Rakoczy, Elizabeth P; Li, Fan; Alarcon-Martinez, Luis; Gonzalez-Cordero, Anai; Bui, Bang V; Liu, Guei-Sheung