日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Reducing clinical trial eligibility barriers for patients with MDS: an icMDS position statement

降低MDS患者参与临床试验的门槛:icMDS立场声明

Borate, Uma; Pugh, Kelly; Waller, Allyson; Welkie, Rina Li; Huang, Ying; Bewersdorf, Jan Philipp; Stahl, Maximilian; DeZern, Amy E; Platzbecker, Uwe; Sekeres, Mikkael A; Wei, Andrew H; Buckstein, Rena J; Roboz, Gail J; Savona, Michael R; Loghavi, Sanam; Hasserjian, Robert P; Fenaux, Pierre; Sallman, David A; Hourigan, Christopher S; Della Porta, Matteo Giovanni; Nimer, Stephen; Little, Richard F; Santini, Valeria; Efficace, Fabio; Taylor, Justin; Garcia-Manero, Guillermo; Odenike, Olatoyosi; Kim, Tae Kon; Halene, Stephanie; Komrokji, Rami S; Griffiths, Elizabeth A; Greenberg, Peter L; Xu, Mina L; Xie, Zhuoer; Bejar, Rafael; Sanz, Guillermo F; Patnaik, Mrinal M; Figueroa, Maria; Carraway, Hetty E; Abdel-Wahab, Omar; Starczynowski, Daniel; Padron, Eric; Boultwood, Jacqueline; Gore, Steven; Daver, Naval G; Churpek, Jane E; Majeti, Ravindra; Bennett, John M; List, Alan F; Brunner, Andrew M; Zeidan, Amer M

Long-term follow-up and combined Phase 2 results of eprenetapopt and azacitidine in patients with TP53 mutant MDS/AML

长期随访及eprenetapopt联合阿扎胞苷治疗TP53突变型MDS/AML患者的II期联合试验结果

Sallman, David A; Komrokji, Rami S; Dezern, Amy E; Sebert, Marie; Garcia-Manero, Guillermo; Rahmé, Ramy; Winer, Eric S; Lehmann-Che, Jacqueline; Roboz, Gail J; Madelaine, Isabelle; Sekeres, Mikkael A; Peterlin, Pierre; Chan, Onyee; Beyne-Rauzy, Odile; Kuykendall, Andrew; Recher, Christian; McLemore, Amy; Stamatoullas, Aspasia; Zhang, Ling; Willems, Lise; Mo, Qianxing; Raffoux, Emmanuel; Nardelli, Lisa; Berthon, Céline; Al Ali, Najla H; Quesnel, Bruno; Padron, Eric; Kantarjian, Hagop M; List, Alan F; Ades, Lionel; Lancet, Jeffrey E; Fenaux, Pierre; Cluzeau, Thomas

Biological drivers of clinical phenotype in myelofibrosis

骨髓纤维化临床表型的生物学驱动因素

Mascarenhas, John; Gleitz, Hélène F E; Chifotides, Helen T; Harrison, Claire N; Verstovsek, Srdan; Vannucchi, Alessandro Maria; Rampal, Raajit K; Kiladjian, Jean-Jacques; Vainchenker, William; Hoffman, Ronald; Schneider, Rebekka K; List, Alan F

An agenda to advance research in myelodysplastic syndromes: a TOP 10 priority list from the first international workshop in MDS

推进骨髓增生异常综合征研究的议程:首届国际骨髓增生异常综合征研讨会提出的十大优先事项清单

Stahl, Maximilian; Abdel-Wahab, Omar; Wei, Andrew H; Savona, Michael R; Xu, Mina L; Xie, Zhuoer; Taylor, Justin; Starczynowski, Daniel; Sanz, Guillermo F; Sallman, David A; Santini, Valeria; Roboz, Gail J; Patnaik, Mrinal M; Padron, Eric; Odenike, Olatoyosi; Nazha, Aziz; Nimer, Stephen D; Majeti, Ravindra; Little, Richard F; Gore, Steven; List, Alan F; Kutchroo, Vijay; Komrokji, Rami S; Kim, Tae Kon; Kim, Nina; Hourigan, Christopher S; Hasserjian, Robert P; Halene, Stephanie; Griffiths, Elizabeth A; Greenberg, Peter L; Figueroa, Maria; Fenaux, Pierre; Efficace, Fabio; DeZern, Amy E; Della Porta, Matteo G; Daver, Naval G; Churpek, Jane E; Carraway, Hetty E; Brunner, Andrew M; Borate, Uma; Bennett, John M; Bejar, Rafael; Boultwood, Jacqueline; Loghavi, Sanam; Bewersdorf, Jan Philipp; Platzbecker, Uwe; Steensma, David P; Sekeres, Mikkael A; Buckstein, Rena J; Zeidan, Amer M

A macaque clonal hematopoiesis model demonstrates expansion of TET2-disrupted clones and utility for testing interventions

猕猴克隆造血模型展示了TET2破坏克隆的扩增及其在测试干预措施方面的应用价值

Shin, Tae-Hoon; Zhou, Yifan; Chen, Shirley; Cordes, Stefan; Grice, Max Z; Fan, Xing; Lee, Byung-Chul; Aljanahi, Aisha A; Hong, So Gun; Vaughan, Kelli L; Mattison, Julie A; Kohama, Steven G; Fabre, Margarete A; Uchida, Naoya; Demirci, Selami; Corat, Marcus A F; Métais, Jean-Yves; Calvo, Katherine R; Buscarlet, Manuel; Natanson, Hannah; McGraw, Kathy L; List, Alan F; Busque, Lambert; Tisdale, John F; Vassiliou, George S; Yu, Kyung-Rok; Dunbar, Cynthia E

P1282: DISEASE-SPECIFIC U1 SPLICEOSOMAL RNA MUTATIONS IN MATURE B-CELL NEOPLASMS

P1282:成熟B细胞肿瘤中疾病特异性U1剪接体RNA突变

Oerlemans, Simone; Bennink, M Christine; Levin, Mark David; Broijl, Annemiek; Van der Klift, Marjolein; Van Deursen, Judith; Vogels, Daphne; Van de Poll-Franse, Lonneke V; Sonneveld, Pieter; Hazelzet, Jan A; Tick, Lidwine W; Seguí, Inés Gómez; Aracil, Eva Frances; Eva, Mingot-Castellano Maria; Pampliega, M Vara; Goterris, Rosa; Candel, F García; Izquierdo, Cristina Pascual; Garma, Julio del Rio; Dominguez, Luisa Guerra; Andrés, Isabel Vicuña; Peinado, Jose Garcia-Arroba; Marcos, Saioa Zalba; Estevez, Julia Vidan; Gonzalez, Elena; Saavedra, Veronica Campuzano; Gala, Jose Maria Garcia; Sanchez, S Ortega; Nieto, Jorge Martínez; Gambarte, Laura Pardo; Rodríguez, Maria Sole; Docampo, Marta Fernandez; Idrovo, Laura F Ávila; Hernández, Luis M; Cid, Joan; Rubia, Javier DE LA; Groen, Kaz; Stege, Claudia; Nasserinejad, Kazem; de Heer, Koen; van Kampen, Roel JW; Leys, Rineke BL; Thielen, Noortje; Westerman, Matthijs; Wu, Ka-Lung; Ludwig, Inge; Issa, Djamila E; Velders, Gerjo A; Vekemans, Marie-Christiane; van de Donk, Niels WCJ; Timmers, Gert-Jan; de Boer, Fransien; Tick, Lidwine W; van der Spek, Ellen; de Waal, Esther GM; Sohne, Maaike; Sonneveld, Pieter; Nijhof, Inger S; Klein, Saskia K; Levin, Mark-David; Ypma, Paula F; Zweegman, Sonja; Montesinos, Pau; Rodríguez-Veiga, Rebeca; Bergua Burgues, Juan Miguel; Algarra, Lorenzo; Botella, Carmen; Josè Antonio, Perez Simon; Bernal, Teresa; Tormo, Mar; Robles, Maria Calbacho; Salamero, Olga; Serrano, Josefina; Noriega, Victor; López-López, Juan Antonio; Polo, Susana Vives; Colorado, Mercedes; Lorenzo, Jose Luis Lopez; Vidriales, María Belén; Boyero, Raimundo Garcia; Olave, Mayte; Herrera-Puente, Pilar; Arce, Olga; Garcia, Manuel Barrios; Jose Sayas Lloris, Maria; Polo, Marta; Isabel Gomez Roncero, Maria; Barragan, Eva; Ayala Diaz, Rosa; Carmen Chillon, Maria; Jose Calasanz, Maria; Boluda, Blanca; Martinez-Cuadrón, David; Labrador, Jorge; Komrokji, Rami S; Ball, Somdeb; Maggioni, Giulia; Travaglino, Erica; Al Ali, Najla; Fenaux, Pierre; Platzbecker, Uwe; Santini, Valeria; Díez Campelo, María; Haferlach, Torsten; Singh, Avani; Jain, Akriti; Aguirre, Luis E; Tinsley, Sara; Schwabkey, Zaker; Chan, Onyee; Xie, Zhuoer; Brunner, Andrew; Kuykendall, Andrew; Bennett, John; Buckstein, Rena; Bejar, Rafael; Bewersdorf, Jan; Carraway, Hetty; Dezern, Amy; Griffiths, Elizabeth A; Halene, Stephanie; Hasserjian, Robert Paul; Loghavi, Sanam; Odenike, Olatoyosi; Patnaik, Mrinal; Roboz, Gail; Stahl, Maximillian; Sekeres, Mikkael; Steensma, David; Savona, Michael Robert; Taylor, Justin; Xu, Mina; Sweet, Kendra; Lancet, Jeffrey; List, Alan; Padron, Eric; Sallman, David; Zeidan, Amer M; Della Porta, Matteo Giovanni; Nadeu, F; Shuai, S; Clot, G; Hilton, L K; Diaz-Navarro, A; Martín, S; Royo, R; Baumann, T; Kulis, M; López-Oreja, I; Cossio, M; Lu, J; Ljungström, V; Young, E; Plevova, K; Knisbacher, B A; Lin, Z; Hahn, C K; Bousquets, P; Alcoceba, M; González, M; Colado, E; Aymerich, M; Terol, M J; Rivas-Delgado, A; Enjuanes, A; Ruiz-Gaspà, S; Chatzikonstantinou, T; Hägerstrand, D; Jylhä, C; Skaftason, A; Mansouri, L; Stranska, K; Doubek, M; van Gastel-Mol, E J; Davis, Z; Walewska, R; Scarfò, L; Trentin, L; Visentin, A; Parikh, S A; Rabe, K G; Moia, R; Armand, M; Rossi, D; Davi, F; Gaidano, G; Kay, N E; Shanafelt, T; Ghia, P; Oscier, D; Langerak, A W; Beà, S; López-Guillermo, A; Neuberg, D; Wu, C J; Getz, G; Pospisilova, S; Stamatopoulos, K; Rosenquist, R; Huber, W; Zenz, T; Colomer, D; Martín-Subero, J I; Delgado, J; Morin, R D; Stein, L D; Puente, X S; Campo, E

Dual pyroptotic biomarkers predict erythroid response in lower-risk non-del(5q) myelodysplastic syndromes treated with lenalidomide and recombinant erythropoietin

双重细胞焦亡生物标志物可预测接受来那度胺和重组人红细胞生成素治疗的低危非del(5q)骨髓增生异常综合征患者的红系反应

Wang, Chen; McGraw, Kathy L; McLemore, Amy F; Komrokji, Rami; Basiorka, Ashley A; Al Ali, Najla; Lancet, Jeffrey E; Padron, Eric; Kosmider, Olivier; Fontenay, Michaela; Fenaux, Pierre; List, Alan F; Sallman, David A

Eprenetapopt (APR-246) and Azacitidine in TP53-Mutant Myelodysplastic Syndromes

Eprenetapopt (APR-246) 和阿扎胞苷治疗 TP53 突变型骨髓增生异常综合征

Sallman, David A; DeZern, Amy E; Garcia-Manero, Guillermo; Steensma, David P; Roboz, Gail J; Sekeres, Mikkael A; Cluzeau, Thomas; Sweet, Kendra L; McLemore, Amy; McGraw, Kathy L; Puskas, John; Zhang, Ling; Yao, Jiqiang; Mo, Qianxing; Nardelli, Lisa; Al Ali, Najla H; Padron, Eric; Korbel, Greg; Attar, Eyal C; Kantarjian, Hagop M; Lancet, Jeffrey E; Fenaux, Pierre; List, Alan F; Komrokji, Rami S

Lenalidomide-Epoetin Alfa Versus Lenalidomide Monotherapy in Myelodysplastic Syndromes Refractory to Recombinant Erythropoietin

来那度胺-促红素α联合疗法与来那度胺单药疗法治疗对重组促红素治疗无效的骨髓增生异常综合征的疗效比较

List, Alan F; Sun, Zhuoxin; Verma, Amit; Bennett, John M; Komrokji, Rami S; McGraw, Kathy; Maciejewski, Jaroslaw; Altman, Jessica K; Cheema, Puneet S; Claxton, David F; Luger, Selina M; Mattison, Ryan J; Wassenaar, Timothy R; Artz, Andrew S; Schiffer, Charles A; Litzow, Mark R; Tallman, Martin S

Integrated Human and Murine Clinical Study Establishes Clinical Efficacy of Ruxolitinib in Chronic Myelomonocytic Leukemia

一项整合了人类和小鼠的临床研究证实了鲁索替尼治疗慢性粒单核细胞白血病的临床疗效。

Hunter, Anthony M; Newman, Hannah; Dezern, Amy E; Steensma, David P; Niyongere, Sandrine; Roboz, Gail J; Mo, Qianxing; Chan, Onyee; Gerds, Aaron; Sallman, David A; Dominguez-Viqueira, William; Letson, Christopher; Balasis, Maria E; Ball, Markus; Kruer, Traci; Zhang, Hailing; Lancet, Jeffrey E; List, Alan F; Sekeres, Mikkael A; Komrokji, Rami S; Padron, Eric