Niemann Pick C1 mistargeting disrupts lysosomal cholesterol homeostasis contributing to neurodegeneration in a Batten disease model.
尼曼匹克 C1 错误靶向会破坏溶酶体胆固醇稳态,从而导致巴顿病模型中的神经退行性变
期刊:Science Advances
影响因子:12.5
doi:10.1126/sciadv.adr5703
Appu Abhilash P, Bagh Maria B, Plavelil Nisha, Mondal Avisek, Sadhukhan Tamal, Singh Satya P, Perkins Neil J, Liu Aiyi, Mukherjee Anil B