TRLS-08. ROVER: A PHASE 1/2 TRIAL IN PROGRESS OF AVAPRITINIB IN PEDIATRIC PATIENTS WITH SOLID TUMORS DEPENDENT ON KIT OR PDGFRA SIGNALING
TRLS-08. ROVER:一项针对KIT或PDGFRA信号通路依赖性实体瘤患儿的Avapritinib 1/2期临床试验正在进行中
期刊:Cureus Journal of Medical Science
影响因子:1.3
doi:10.7759/cureus.62972
Perry, Isaac E; Staursky, Daniel; Asfari, Mohammad Maysara; Vega, Kenneth J; Das, Anirban; Fernandez, Nicholas R; Bielamowicz, Kevin J; Abebe-Campino, Gadi; Caspi, Shani; Per, Nyman; Graham, Richard T; Kim, John Y; Wilhelmsson, Mari; Jorgensen, Mette; Michaeli, Orli; Fernández, Maria Baro; Li, Amanda; Levine, Adrian; Aamir, Zoya; Stengs, Lucie; Negm, Logine; Bianchi, Vanessa; Edwards, Melissa; Bennett, Julie; Ertl-Wagner, Birgit; Dirks, Peter; Bouffet, Eric; Hawkins, Cynthia; Tabori, Uri; Massimino, Maura; Biassoni, Veronica; Mastronuzzi, Angela; Schiavello, Elisabetta; Barretta, Francesco; Quaglietta, Lucia; Milanaccio, Claudia; Pecori, Emilia; Cacchione, Antonella; Ruscio, Valentina Di; Chiesa, Silvia; Scimone, Giuseppe; Barra, Salvina; De Martino, Lucia; Nigro, Olga; Ramaglia, Antonia; Picariello, Stefania; Verrico, Antonio; Vallero, Stefano; Mussano, Anna; Vennarini, Sabina; Calareso, Giuseppina; Podda, Marta; Gattuso, Giovanna; Cinalli, Giuseppe; Antonelli, Manila; Dossena, Chiara; Buttarelli, Francesca Romana; Gianno, Francesca; Minasi, Simone; Modena, Piergiorgio; De Cecco, Loris; Senapati, Akanksha; Lindsay, Holly; Gilheeney, Stephen; Bale, Tejus; Taylor, Michael; Khuong-Quang, Dong-Anh; Bouffet, Eric; Khan, Sara; van Veelan, Marie-Lise; Kros, Johan M; Vasiljevic, Alexandre; Pollack, Ian; Chambless, Lola; Gupta, Nalin; Weiss, William A; Jabado, Nada; Sterba, Jaroslav; Zapotocky, Michal; Hansford, Jordan R; Ramaswamy, Vijay; Mariet, Cassandra; Tauziède-Espariat, Arnault; Auffret, Lucie; Ajlil, Yassine; Roux, Alexandre; Pallud, Johan; Palfi, Stéphane; Métais, Alice; Beccaria, Kevin; Blauwblomme, Thomas; Puget, Stéphanie; Sanson, Marc; Peloux, Marie; Richard, Juliette; Thalhammer, Julian; Carvalho, Alice; Puiseux, Chloé; Pereira, Victor; de Carli, Emilie; Lesieur, Thomas; Rouger, Jeremie; Page, Philipe; Doz, François; Bourdeaut, Franck; Dufour, Christelle; Abou, Samuel; Guerrini-Rousseau, Léa; Dhermain, Frédéric; Bolle, Stéphanie; Varlet, Pascale; Grill, Jacques; Castel, David; Joshi, Piyush; Stelzer, Tamina; Okonechnikov, Konstantin; Sarropoulos, Ioannis; Sepp, Mari; Pour-Jamnani, Mischan V; Rademacher, Anne; Yamada-Saito, Tetsuya; Schneider, Céline; Schmidt, Julia; Schäfer, Philipp; Leiss, Kevin; Bortolomeazzi, Michele; Mallm, Jan-Philipp; da Silva, Patricia B G; Statz, Britta; Wittmann, Andrea; Schramm, Kathrin; Blattner-Johnson, Mirjam; Fiesel, Petra; Jones, Barbara; Milde, Till; Pajtler, Kristian; van Tilburg, Cornelis M; Witt, Olaf; Rippe, Karsten; Korshunov, Andrey; Jones, David T W; Hovestadt, Volker; Northcott, Paul A; Thongjuea, Supat; Jäger, Natalie; Kaessmann, Henrik; Pfister, Stefan M; Kutscher, Lena M; Traunwieser, Thomas; Loos, Elena; Ottensmeier, Holger; Mynarek, Martin; Bison, Brigitte; Kandels, Daniela; Rossius, Anne; Lüttich, Peggy; Baust, Katja; Faulstich-Ritter, Kristin; John, Rainer; Kreisch, Andrea; Landmann, Judyta; Manteufel, Eva; Nest, Alexandra; Prüfe, Jenny; Schubert, Lisa; Stamm, Walther; Timmermann, Beate; Gerss, Joachim; Rutkowski, Stefan; Schlegel, Paul-Gerhardt; Eyrich, Matthias; Gnekow, Astrid K; Frühwald, Michael C; Massimino, Maura; Dossena, Chiara; Minasi, Francesco; Barretta, Francesco; Buttarelli, Francesca Romana; Biassoni, Veronica; Oriani, Matilde; Schiavello, Elisabetta; Ficorilli, Marica; Nigro, Olga; Pollo, Bianca; Antonelli, Manila; Donofrio, Vittoria; Maggioni, Marco; Kool, Marcel; Pecori, Emilia; Vennarini, Sabina; Gianno, Francesca; nigro, olga; Erbetta, Alessandra; Chiapparini, Luisa; Luksch, Roberto; Barzanò, Elena; Meazza, Cristina; Podda, Marta; Spreafico, Filippo; Terenziani, Monica; Bergamaschi, Luca; Ferrari, Andrea; Casanova, Michela; Chiaravalli, Stefano; Gattuso, Giovanna; Bailey, Simon; Modena, Piergiorgio; De Cecco, Loris; Tao, Ran; Erkek, Serap; Matsui, Yurika; Xu, Beisi; Smith, Kyle S; Gao, Qingsong; Li, Yiran; Djekidel, Nadhir; Darrow, Emily; Kumar, Rahul; Paul, Leena; Lin, Hong; Hadley, Jennifer; Batts, Melissa; Bhanu, Natarajan V; Kutscher, Lena; Garcia, Benjamin A; Zhou, Xin; Orr, Brent A; Robinson, Giles W; Wu, Gang; Korbel, Jan O; Peng, Jamy; Pfister, Stefan M; Northcott, Paul A; Öz, Elif; Hardt, Annika; Kortmann, Rolf-Dieter; Schwarz, Rudolf; Timmermann, Beate; Bison, Brigitte; Warmuth-Metz, Monika; von Hoff, Katja; von Bueren, André O; Gerber, Nicolas U; Fleischhack, Gudrun; Pietsch, Torsten; Pfister, Stefan M; Sturm, Dominik; Mynarek, Martin; Rutkowski, Stefan; Obrecht-Sturm, Denise; Deghedy, Marwa; English, Martin; Curry, Helen; Nicholson, James; O’Hare, Patricia; McCarthy, Anthony; Uzunova, Lena; Curry, Sarah; Wilson, Shaun; Jorgensen, Mette; Thompson, Dominic; Cox, Rachel; Ronghe, Milind; Brougham, Mark; McAndrew, Rachel; Lee, Victoria; Bailey, Simon; Thorbinson, Colin; Goodden, John; Picton, Susan; Dias, Sandra; Saeed, Fozia; Srivatsa, Kavitha; Ritzmann, Timothy; Grundy, Richard; Kilday, John-Paul; Lenen, Alicia; Waanders, Angela J; Bazzi, Latifa; Zhang, Hui; Lai, Jin-Shei; Plant-Fox, Ashley S; Cluster, Andrew; Crawford, John; Cohen, Ken; Dickens, David; Dole, Mukund; Goodman, Jessica; Hoffman, Lindsey; Koschmann, Carl; Lazow, Margot; Marks, Asher; Puccetti, Diane; Skrypek, Mary M; Tanaka, Ryuma; Weintraub, Lauren; Wright, Karen; Rush, Sarah Zieber; Fangusaro, Jason; Lulla, Rishi; Goldman, Stewart; Pillay-Smiley, Natasha; Wright-Nadkarni, Mariah L; Moscato, Emily L; Stanek, Joseph R; Schaefer, Megan R; Gerhardt, Cynthia A; Ashley, David M; Baxter, Patricia A; Chi, Susan N; Dorris, Kathleen; Fisher, Michael J; Hummel, Trent R; Hwang, Eugene I; Gass, David; Leary, Sarah E S; Pillay-Smiley, Natasha; Plant, Ashley S; Murala, Mythili; Mikael, Leonie; Fouladi, Maryam; Lazow, Margot A; Fangusaro, Jason; Onar-Thomas, Arzu; Poussaint, Tina Young; Lensing, Shelly; Ligon, Azra H; Lindeman, Neal; Banerjee, Anuradha; Kilburn, Lindsay; Lenzen, Alicia; Pillay-Smiley, Natasha; Pollack, Ian F; Robison, Nathan; Partap, Sonia; Qaddoumi, Ibrahim; Landi, Daniel; Jones, David T W; Stewart, Clinton F; Fouladi, Maryam; Dunkel, Ira J; Levashov, Andrey Sergeevich; Serov, Yuriy Alexandrovich; Ushakova, Tatyana Leonidovna; Stroganova, Anna Mikhailovna; Ryzhova, Marina Vladimirovna; Gorelyshev, Sergey Kirillovich; Kadirov, Shavkat Umidovich; Terentyeva, Alexandra Igorevna; Grigoryeva, Marina Vladimirovna; Polyakov, Vladimir Georgievich; Gorovtsova, Olga Valeryevna; Grigorenko, Vasiliy Andreevich; Laternser, Sandra; De Micheli, Andrea Joseph; Petrovic, Antonela; Brüningk, Sarah; McDonough, Elizabeth; Surrette, Christine; Ginty, Fiona; Eze, Augustine; Dettwiler, Susanne; Prutek, Fabiola; Lagar, Noelia Casares; Morinigo, Denise; Bornhorst, Miriam; Rushing, Elisabeth Jane; Grotzer, Michael; Stücklin, Ana Sofia Guerreiro; Müller, Sabine; Packer, Roger; Rodan, Marta Maria Alonso; Nazarian, Javad; Abu-Arja, Mohammad Hatim; McGlynn, Mary Claire; Zaghloul, Mohammed Saad; Elhemaly, Ahmed; Bertrand, Kelsey; Gajjar, Ammar; Ronsley, Rebecca; Cappellano, Andrea M; Dassi, Natalia; Czogala, Malgorzata; Graham, Richard; Knowles, Truman; Meuller, Sabine; Dhall, Girish; Nagabushan, Sumanth; Abdelbaki, Mohamed S; Bagchi, Aditi; Robinson, Giles W; Desai, Ami V; Wu, Yeming; Wang, Huanmin; Basu, Ellen M; Casanova, Michela; van Tilburg, Cornelis M; Campbell-Hewson, Quentin; Armstrong, Amy E; André, Nicolas; Devlin, Clare; Wulff, Jade; Cardenas, Alison; Hutchinson, Katherine E; Lian, Qinshu; Ryklansky, Carolina; Harmach, Vesna Sneller; Fox, Elizabeth; Gajjar, Amar; Corbett, Ryan J; Kaufman, Rebecca; McQuaid, Shelly W; Vaksman, Zalman; Phul, Saksham; Brown, Miguel A; Mason, Jennifer L; Desai, Heena; Hausler, Ryan; Naqvi, Ammar S; Chroni, Antonia; Geng, Zhuangzhuang; Zhang, Bo; Zhong, Chuwei; Zhu, Yuankun; Heath, Allison P; Li, Marilyn; Storm, Phillip B; Resnick, Adam C; Maxwell, Kara N; Bornhorst, Miriam; Cole, Kristina A; Waanders, Angela J; MacFarland, Suzanne P; Rokita, Jo Lynne; Diskin, Sharon J; Wong, Kendrew S K; Patel, Samir; Lafay-Cousin, Lucie; Logie, Natalie; D’Alessandro, Paul; Magimairajan, Vanan; Cacciotti, Chantel; Perreault, Sebastien; Alves, Melanie; Galopin, Marie; Poirier, Éloise; Skamene, Sonia; Bergeron-Gravel, Samuel; Lagacé, Simon; Charpentier, Anne-Marie; Erker, Craig; Crooks, Bruce; Rutledge, Rob; Sandhu, Ash; Brooks, Beth; Lo, Andrea C; Tsang, Derek S; Cheng, Sylvia; Mynarek, Martin; Doz, Francois; Clifford, Steve C; Bailey, Simon; Rutkowski, Stefan; Padovani, Laeticia; Bouchoucha, Yassine; Partanen, Marita; Verity, Sarah; Sehested, Astrid; Puhr, Anita; Rossius, Anne; Chevignard, Mathilde; Dorfer, Christian; Damaty, Ahmed El; Beccaria, Kevin; Aquilina, Kristian; Hoving, Eelco W; Schuhmann, Martin U; Thomale, Ulrich W; Milde, Till; Pillay-Smiley, Natasha; Nussbaumer, Gunther; Damen-Corbijn, Carin; Baugh, Joshua; Webster, Aaron; Lane, Adam; Godschalk, T C; Grill, Jacques; Hawkins, Cynthia; Leach, James; Janssens, Geert; Jones, Blaise; Massimino, Maura; Karremann, Michael; van Vuurden, Dannis G; Bailey, Simon; Das, Anirban; Thomale, Ulrich-Wilhelm; Goldman, Stewart; Perreault, Sebastien; Biassoni, Veronica; Minturn, Jane; Hummel, Trent; Kramm, Christof; van Zanten, Sophie Veldhuijzen; Hoffman, Lindsey M; Cansanay, Rose Daynielle; Erker, Craig; Ratterman, Erin; Schlosser, Mary Pat; Ronsley, Rebecca; Cacciotti, Chantel; Hukin, Juliette; Cheng, Sylvia; Pillay-Smiley, Natasha; Magimairajan, Vanan; Cluster, Andrew; Abdelbaki, Mohamed S; Margol, Ashley; Michael, George; Chi, Susan; Salloum, Ralph; Ramaswamy, Vijay; Zapotocky, Michal; Lopez, Vicente Santa Maria; Toledano, Helene; Dorris, Kathleen; Mynarek, Martin; Rutkowski, Stefan; Lassaletta, Alvaro; Bouffet, Eric; Lafay-Cousin, Lucie; Perwein, Thomas; Nussbaumer, Gunther; Filipek, Iwona; Piccolo, Gianluca; Garrè, Maria Luisa; Castellano, Serafin; Lassaletta, Alvaro; Salvador, Hector; Baroni, Lorena; Valera, Elvis Terci; Scrideli, Carlos; Jónsson, Ólafur G; Scheinemann, Katrin; Kilday, John-Paul; Thomas, Christian; Hasselblatt, Martin; Kordes, Uwe R; Adamski, Jenny; Benesch, Martin; Obrecht-Sturm, Denise; Mobarak, Nahla Aly; Balbaid, Ali Abdullah O; Alotabi, Fahad; Banyan, Ayman Al; Alluhaybi, Abdulelah A; Ahmad, Maqsood; AlYahya, Amal S; AlYamany, Basma Mahmoud; Shakweer, Wafa Al; Abedalthagafi, Malak; Al-Dandan, Sadeq; Aljabarat, Wael; AlNaqib, Zaid G; Rayis, Mohammed; Alharbi, Musa; de la Peña-Hernández, Beth Sainz; Arreguín-González, Farina; Valdéz-Orduño, Ricardo; Almazán-García, Blanca; Sandoval-de Jesús, San Juanita; Baños-Rodríguez, Eduardo; López-Azcárraga, Alejandra; García-Ramos, Jeannie; Sebastian-Barajas, Ruben; Ochoa-Madrigal, Georgina; Moreira, Daniel; Benito-Reséndiz, Alma; Liu, Anthony P Y; Yan, Carol L S; Cheng, P W; Lo, S S M; Chow, Terry T W; Fu, Eric C H; Yau, Jeffrey P W; Lee, Vincent; Chan, Godfrey C F; Ku, Dennis T L; Shing, Matthew M K; Siu, Deyond Y W; Arce-Cabrera, Daniela; Escamilla-Asiain, Gabriela; Nájera-Castillo, Melisa; del Campo, Regina Navarro-Martín; Ortiz-Azpilcueta, Mariana; Pantoja-Guillén, Francisco; González, Farina Arreguín; Zapata-Sosa, Imelda; Lugo-Juárez, Jocelyn; Santillán-Cortés, Daniel; La Madrid, Andrés Morales-; Moreira, Daniel; Benito-Reséndiz, Alma; Bruckner, Katharina; Lötsch-Gojo, Daniela; Gabler, Lisa; Wang, Shanzheng; Kirchhofer, Dominik; Labelle, Jenna; Madlener, Sibylle; Senfter, Daniel; Schmitt-Hoffner, Felix; Federico, Aniello; Koster, Jan; Dorfer, Christian; Tauziède-Espariat, Arnault; Pahnke, Jens; Hovestadt, Volker; Beck, Alexander; Schueler, Julia; Haberler, Christine; Berger, Walter; Filbin, Mariella G; Kool, Marcel; Gojo, Johannes; Gudenas, Brian; Englinger, Bernhard; Liu, Anthony P Y; Ahmad, Sheikh Tanveer; Zhao, Miao; Meredith, David; Pfaff, Elke; Paul, Leena; Hadley, Jennifer; Batts, Melissa; Klimo Jr., Paul; Boop, Frederick A; Gajjar, Amar; Robinson, Giles W; Orr, Brent A; Lin, Hong; Alexandrescu, Sanda; Jones, David T W; Swartling, Fredrik; Filbin, Mariella G; Northcott, Paul A; Panizo, Elena; Vazquez-Gomez, Felisa; Perez-Somarriba, Marta; Cruz, Ofelia; Lopez-Ibor, Blanca; Solano, Palma; De las Heras, Blanca Martinez-; Cortés-Hernandez, Marta; Garcia-Ariza, Miguel; Raynero-Mellado, Roberto Carlos; Martinez-Merino, Marta; De Lucio, Ana; Tallón, María; Garrido-Colino, Carmen; Ortiz-Gonzalez, Irene; Portugal, Raquel; Baro, Maria; Gonzalez-Sansegundo, Carmen; Calvo, Felipe; Lassaletta, Alvaro; Carmona, Enrique Blanco; Paassen, Irene; He, Jiayou; Büllesbach, Annette; Buhl, Juliane L; Federico, Aniello; Liu, Ilon; Young, Matthew; Kildisiute, Gerda; Behjati, Sam; Vibhakar, Rajeev; Donson, Andrew; Foreman, Nicholas; Hovestadt, Volker; Shaw, McKenzie; Chi, Susan N; Frühwald, Michael; Korshunov, Andrey; Hasselblatt, Martin; Hoving, Eelco W; Jäger, Natalie; Johann, Pascal D; Pfister, Stefan M; Filbin, Mariella; Drost, Jarno; Kool, Marcel; Boisvert, Michelle; Perera, Ashwyn A; Jeang, John; Condurat, Alexandra L; Tsai, Jessica W; Novikov, Dana; Collins, Jared; Morin, Eric; Woods, Jared; Zhou, Kevin; Chacon, Madison; DiGiacomo, Jeromy; Kumbhani, Rushil; Wang, Dayle; Taylor, Michael D; Hansford, Jordan R; Ludlow, Louise E A; Jabado, Nada; Ligon, Keith L; Beroukhim, Rameen; Bandopadhayay, Pratiti; Jones, David T W; Gajjar, Amar J; Orr, Brent; Ellison, David; Lafay-Cousin, Lucie; Minturn, Jane; Fisher, Michael; Bendel, Anne; Hwang, Eugene; Murray, Jeffrey; Landi, Daniel; Smith, Amy; Gottardo, Nicholas; Valvi, Santhosh; Hassal, Tim; Elster, Jennifer; Perrault, Sebastian; Ramaswamy, Vijay; Partap, Sonia; Laughton, Stephen; Cohn, Richard; Chintagumpala, Murali; McCowage, Geoffrey; Hansford, Jordan; Sullivan, Michael; Sayour, Elias; Bowers, Daniel; Marks, Asher; Huang, Jie; Lucas, John; Tinkle, Christopher; Pinto, Soniya; Bag, Asim; Sabin, Noah; Northcott, Paul; Klimo, Paul; Merchant, Thomas E; Onar-Thomas, Arzu; Robinson, Giles W; Abbou, Samuel; Koschmann, Carl; Kramm, Christof M; Hoffman, Lindsey M; Plant-Fox, Ashley S; Abdelbaki, Mohamed S; Bui, Ashley; Casanova, Michela; van Tilburg, Cornelis M; Khuong-Quang, Dong-Anh; Chi, Susan N; Shi, Hongliang; Bidollari, Ilda; Hong, Janet; Swamy, Preethi; Roche, Maria; Morgenstern, Daniel A