日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

CD19 CAR-T cells for treatment-refractory autoimmune diseases: the phase 1/2 CASTLE basket trial

CD19 CAR-T 细胞治疗难治性自身免疫性疾病:CASTLE 篮子试验(1/2 期)

Müller, Fabian; Hagen, Melanie; Wirsching, Andreas; Kharboutli, Soraya; Aigner, Michael; Völkl, Simon; Kretschmann, Sascha; Tascilar, Koray; Taubmann, Jule; Bucci, Laura; Raimondo, Maria Gabriella; Bergmann, Christina; Rothe, Tobias; Corte, Giulia; Tur, Carlo; Muñoz, Luis; Böltz, Sebastian; Schuster, Louis; Hartmann, Fabian; Garantziotis, Panagiotis; Spörl, Silvia; Vasova, Ingrid; Gerbitz, Armin; Spriewald, Bernd; Kiener, Hans; Giannarelli, Diana; Locatelli, Franco; D'Agostino, Maria-Antonietta; Hanssens, Linda; Miltenyi, Stefan; Bozec, Aline; Grieshaber-Bouyer, Ricardo; Mackensen, Andreas; Schett, Georg

Sustained Benefit of Blinatumomab in Infants With KMT2A-Rearranged ALL: Long-Term Outcomes, Toxicity, and Pharmacokinetics

Blinatumomab 对 KMT2A 重排 ALL 患儿的持续疗效:长期结果、毒性和药代动力学

Vieira Martins, Miguel; de Lorenzo, Paola; Kotecha, Rishi S; Attarbaschi, Andishe; Escherich, Gabriele; Nysom, Karsten; Stary, Jan; Ferster, Alina; Brethon, Benoit; Locatelli, Franco; Schrappe, Martin; Scholte-van Houtem, Peggy E; Valsecchi, Maria G; Huitema, Alwin D R; Pieters, Rob; van der Sluis, Inge M

ADAR2 induces the differentiation of osteosarcoma cells by editing activity on IGFBP7: new implications for therapy

ADAR2通过编辑IGFBP7诱导骨肉瘤细胞分化:对治疗的新启示

Rossi, Michela; Scotto di Carlo, Federica; Di Gregorio, Jacopo; Russo, Sharon; Di Giuseppe, Laura; Battafarano, Giulia; Terreri, Sara; Pagliarosi, Olivia; Silvestris, Domenico Alessandro; Corona, Marco; Barra, Adriano; Pezzullo, Marco; De Stefanis, Cristiano; Pelle, Simone; Costici, Pier Francesco; Minisola, Salvatore; Pepe, Jessica; Locatelli, Franco; Gianfrancesco, Fernando; Gallo, Angela; Del Fattore, Andrea

Blinatumomab consolidation in children with high-risk first-relapse B-cell precursor acute lymphoblastic leukemia: final 5-year follow-up analysis of a randomized multicenter phase 3 study

Blinatumomab巩固治疗高危首次复发B细胞前体急性淋巴细胞白血病患儿:一项随机多中心3期研究的最终5年随访分析

Locatelli, Franco; Rizzari, Carmelo; Gruhn, Bernd; Klingebiel, Thomas; Parasole, Rosanna; Linderkamp, Christin; Flotho, Christian; Petit, Arnaud; Micalizzi, Concetta; Eckert, Cornelia; Möricke, Anja; Sartor, Mary; Hrusak, Ondrej; Peters, Christina; Saha, Vaskar; Vinti, Luciana; Desai, Rajendra; Henry, Michael; Zugmaier, Gerhard; von Stackelberg, Arend

Discovery of a new selective ERAP1 inhibitor for Hedgehog-dependent cancer treatment

发现一种新的选择性ERAP1抑制剂,用于治疗Hedgehog依赖性癌症

Bufalieri, Francesca; Cucinotta, Antonino; Cammarone, Silvia; Agnoli, Francesca; Basili, Irene; Ferri, Giulia; Quaglio, Deborah; Caimano, Miriam; Capriotti, Anna Laura; Montone, Carmela Maria; Lospinoso Severini, Ludovica; Tempora, Patrizia; D'Amico, Silvia; Juretich, Francesca; Semrau, Marta S; Navacci, Shirin; Conenna, Marilisa; Bordone, Rosa; Spallotta, Francesco; Garavaglia, Silvia; Storici, Paola; Ghirga, Francesca; Laganà, Aldo; Locatelli, Franco; Ayrault, Olivier; Infante, Paola; Botta, Bruno; Mori, Mattia; Fruci, Doriana; Di Marcotullio, Lucia

DNA Methylation Episignature as a Novel Diagnostic Tool for Diamond-Blackfan Anemia Syndrome

DNA甲基化表观遗传特征作为Diamond-Blackfan贫血综合征的新型诊断工具

Quarello, Paola; Karimi, Karim; Trajkova, Slavica; Garelli, Emanuela; Samadieh, Mehdi; Iovino, Emanuela; Pippucci, Tommaso; Papagni, Giovanni; Dalfonso, Sandra; Corrado, Lucia; Rizzo, Serena; Carando, Adriana; Kerkhof, Jennifer; Rzasa, Jessica; McConkey, Haley; Levy, Michael; Zecca, Marco; Fioredda, Francesca; Barone, Angelica; Cesaro, Simone; Gabelli, Maria; Torchio, Francesca; Zucchetti, Giulia; Cantarini, Maria Elena; Corti, Paola; Ramenghi, Ugo; Locatelli, Franco; Fagioli, Franca; Sadikovic, Bekim; Brusco, Alfredo

Impact of minimal residual disease on the outcome of hematopoietic stem cell transplantation for childhood acute lymphoblastic leukemia within the FORUM trial

FORUM试验中微小残留病灶对儿童急性淋巴细胞白血病造血干细胞移植疗效的影响

Balduzzi, Adriana; Glogova, Evgenia; Peters, Christina; Sedlacek, Petr; Dalle, Jean-Hugues; Locatelli, Franco; Meisel, Roland; Burkhardt, Birgit; Buechner, Jochen; Wachowiak, Jacek; Bierings, Marc; Staciuk, Raquel; Graphakos, Stelios; Güngör, Tayfun; Yesilipek, Akif; Svec, Peter; Palma, Julia; Krivan, Gergely; Diaz-de-Heredia, Cristina; Limido, Francesca; Ansari, Marc; Kalwak, Krzysztof; Bader, Peter; Ifversen, Marianne

Extracellular vesicles from activated Vδ2 T cells inhibit viral replication and enhance adaptive antiviral immunity

活化的Vδ2 T细胞释放的细胞外囊泡可抑制病毒复制并增强适应性抗病毒免疫力。

Bordoni, Veronica; Guarracino, Federica; Marocco, Francesco; Quattrocchi, Luca; Lorusso, Angela; Minutolo, Antonella; Garbo, Sabrina; Pellegrino, Marsha; Vinci, Mara; Matteucci, Claudia; Pagliara, Daria; Galaverna, Federica; Merli, Pietro; Battistelli, Cecilia; Locatelli, Franco; Agrati, Chiara

Comparable outcomes of HSCT up-front and after failure of IST in pediatric aplastic anemia in recent years

近年来,儿童再生障碍性贫血患者接受造血干细胞移植(HSCT)治疗,无论是否先进行免疫抑制治疗(IST),其疗效均相当。

Andresen, Felicia; Yoshimi, Ayami; Bader, Peter; Bierings, Marc; Bod'ová, Ivana; Bordon, Victoria; Buechner, Jochen; Burkhardt, Birgit; Dworzak, Michael; Erlacher, Miriam; Kállay, Krisztián; Labarque, Veerle; Locatelli, Franco; Malone, Andrea; Masmas, Tania; Müller, Ingo; Nöllke, Peter; Schmugge, Markus; Pawelec, Katarzyna; Sedlacek, Petr; Sevilla, Julian; Smith, Owen; Stary, Jan; Niemeyer, Charlotte; Strahm, Brigitte

Advancing precision therapy in pediatric acute myeloid leukemia through PDX models and mitochondrial targeting

通过PDX模型和线粒体靶向治疗推进儿童急性髓系白血病的精准治疗

Da Ros, Ambra; Peloso, Alberto; Longo, Giorgia; Benetton, Maddalena; Indio, Valentina; Cairo, Stefano; Sandri, Monica; Buldini, Barbara; Bresolin, Silvia; Rosato, Antonio; Pession, Andrea; Tregnago, Claudia; Locatelli, Franco; Pigazzi, Martina