Disease Trajectories in the Revised Hammersmith Scale in a Cohort of Untreated Patients with Spinal Muscular Atrophy types 2 and 3
在未经治疗的2型和3型脊髓性肌萎缩症患者队列中,修订版哈默史密斯量表所反映的疾病轨迹
期刊:Journal of Neuromuscular Diseases
影响因子:3.4
doi:10.3233/JND-230211
Wolfe, Amy; Stimpson, Georgia; Ramsey, Danielle; Coratti, Giorgia; Dunaway Young, Sally; Mayhew, Anna; Pane, Marika; Rohwer, Annemarie; Muni Lofra, Robert; Duong, Tina; O'Reilly, Emer; Milev, Evelin; Civitello, Matthew; Sansone, Valeria A; D'Amico, Adele; Bertini, Enrico; Messina, Sonia; Bruno, Claudio; Albamonte, Emilio; Mazzone, Elena; Main, Marion; Montes, Jacqueline; Glanzman, Allan M; Zolkipli-Cunningham, Zarazuela; Pasternak, Amy; Marini-Bettolo, Chiara; Day, John W; Darras, Basil T; De Vivo, Darryl C; Baranello, Giovanni; Scoto, Mariacristina; Finkel, Richard S; Mercuri, Eugenio; Muntoni, Francesco