Nanoparticle delivery of AMPK activator 991 prevents its toxicity and improves muscle homeostasis in Duchenne muscular dystrophy.
纳米颗粒递送 AMPK 激活剂 991 可防止其毒性并改善杜氏肌营养不良症的肌肉稳态。
期刊:Molecular Therapy-Methods & Clinical Development
影响因子:4.7
doi:10.1016/j.omtm.2025.101564
Andreana Ilaria, Ghosh Ananga, Repellin Mathieu, Kneppers Anita, Ben Larbi Sabrina, Tifni Federica, Fessard Aurélie, Martin Marion, Sidi-Boumedine Jacqueline, Kryza David, Stella Barbara, Arpicco Silvia, Bordes Claire, Chevalier Yves, Gondin Julien, Chazaud Bénédicte, Mounier Rémi, Lollo Giovanna, Juban Gaëtan