Editing the Sickle Cell Disease Mutation in Human Hematopoietic Stem Cells: Comparison of Endonucleases and Homologous Donor Templates
编辑人类造血干细胞中的镰状细胞病突变:内切酶和同源供体模板的比较
期刊:Molecular Therapy
影响因子:12.1
doi:10.1016/j.ymthe.2019.05.014
Zulema Romero, Anastasia Lomova, Suzanne Said, Alexandra Miggelbrink, Caroline Y Kuo, Beatriz Campo-Fernandez, Megan D Hoban, Katelyn E Masiuk, Danielle N Clark, Joseph Long, Julie M Sanchez, Miriam Velez, Eric Miyahira, Ruixue Zhang, Devin Brown, Xiaoyan Wang, Yerbol Z Kurmangaliyev, Roger P Hollis