日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Adenine base editing with engineered virus-like particles rescues the CFTR mutation G542X in patient-derived intestinal organoids

利用工程改造的病毒样颗粒进行腺嘌呤碱基编辑,可挽救患者来源的肠道类器官中的 CFTR 突变 G542X。

Lucia Nicosia,Iwona Pranke,Roberta V Latorre,Joss B Murray,Lisa Lonetti,Kader Cavusoglu-Doran,Elise Dreano,James P Costello,Michael Carroll,Paola Melotti,Claudio Sorio,Isabelle Sermet-Gaudelus,Martina F Scallan,Patrick T Harrison

Newborn Screening for Metachromatic Leukodystrophy in Tuscany: The Paradigm of a Successful Preventive Medicine Program

托斯卡纳新生儿异染性脑白质营养不良筛查:成功预防医学项目的典范

Malvagia, Sabrina; Bettiol, Alessandra; Porcaro, Margherita; Mura, Massimo; Funghini, Silvia; Ombrone, Daniela; Forni, Giulia; Scolamiero, Emanuela; Coppi, Filippo; Damiano, Roberta; Cereda, Cristina; Simonetti, Simonetta; Lonetti, Annalisa; Daniotti, Marta; Caciotti, Anna; Morrone, Amelia; Calbi, Valeria; Fumagalli, Francesca; Aiuti, Alessandro; Procopio, Elena; Guerrini, Renzo; la Marca, Giancarlo

Polo-like kinase-1, Aurora kinase A and WEE1 kinase are promising druggable targets in CML cells displaying BCR::ABL1-independent resistance to tyrosine kinase inhibitors

Polo 样激酶 1、Aurora 激酶 A 和 WEE1 激酶是 CML 细胞中有希望的药物靶点,这些细胞对酪氨酸激酶抑制剂表现出 BCR::ABL1 独立的耐药性

Manuela Mancini, Sara De Santis, Cecilia Monaldi, Fausto Castagnetti, Annalisa Lonetti, Samantha Bruno, Elisa Dan, Barbara Sinigaglia, Gianantonio Rosti, Michele Cavo, Gabriele Gugliotta, Simona Soverini

Effect of Hydrophilic Monomer Distribution on Self-Assembly of a pH-Responsive Copolymer: Spheres, Worms and Vesicles from a Single Copolymer Composition

亲水单体分布对pH响应性共聚物自组装的影响:单一共聚物组成形成球状、蠕虫状和囊泡状结构

Zhang, Junliang; Farias-Mancilla, Barbara; Kulai, Ihor; Hoeppener, Stephanie; Lonetti, Barbara; Prévost, Sylvain; Ulbrich, Jens; Destarac, Mathias; Colombani, Olivier; Schubert, Ulrich S; Guerrero-Sanchez, Carlos; Harrisson, Simon

Exploiting Clonal Evolution to Improve the Diagnosis and Treatment Efficacy Prediction in Pediatric AML

利用克隆演化提高儿童急性髓系白血病(AML)的诊断和治疗效果预测

Bertuccio, Salvatore Nicola; Anselmi, Laura; Masetti, Riccardo; Lonetti, Annalisa; Cerasi, Sara; Polidori, Sara; Serravalle, Salvatore; Pession, Andrea

The Glucocorticoid Receptor Polymorphism Landscape in Patients With Diamond Blackfan Anemia Reveals an Association Between Two Clinically Relevant Single Nucleotide Polymorphisms and Time to Diagnosis.

Diamond Blackfan 贫血患者的糖皮质激素受体多态性图谱揭示了两种具有临床意义的单核苷酸多态性与诊断时间之间的关联

Lonetti Annalisa, Indio Valentina, Dianzani Irma, Ramenghi Ugo, Da Costa Lydie, Pospíšilová Dagmar, Migliaccio Anna Rita

hGATA1 Under the Control of a μLCR/β-Globin Promoter Rescues the Erythroid but Not the Megakaryocytic Phenotype Induced by the Gata1 (low) Mutation in Mice

在μLCR/β-珠蛋白启动子控制下的hGATA1可以挽救小鼠Gata1(低表达)突变引起的红系表型,但不能挽救巨核系表型。

Martelli, Fabrizio; Verachi, Paola; Zingariello, Maria; Mazzarini, Maria; Vannucchi, Alessandro M; Lonetti, Annalisa; Bacci, Barbara; Sarli, Giuseppe; Migliaccio, Anna Rita

Insights on the Interplay between Cells Metabolism and Signaling: A Therapeutic Perspective in Pediatric Acute Leukemias

细胞代谢与信号传导相互作用的见解:儿童急性白血病的治疗视角

Anselmi, Laura; Bertuccio, Salvatore Nicola; Lonetti, Annalisa; Prete, Arcangelo; Masetti, Riccardo; Pession, Andrea

Rational design of block copolymer self-assemblies in photodynamic therapy

光动力疗法中嵌段共聚物自组装的合理设计

Demazeau, Maxime; Gibot, Laure; Mingotaud, Anne-Françoise; Vicendo, Patricia; Roux, Clément; Lonetti, Barbara

Inhibition of Methyltransferase DOT1L Sensitizes to Sorafenib Treatment AML Cells Irrespective of MLL-Rearrangements: A Novel Therapeutic Strategy for Pediatric AML

抑制甲基转移酶 DOT1L 可使 AML 细胞对索拉非尼治疗敏感,无论 MLL 重排如何:一种治疗儿童 AML 的新型治疗策略

Annalisa Lonetti, Valentina Indio, Maria Antonella Laginestra, Giuseppe Tarantino, Francesca Chiarini, Annalisa Astolfi, Salvatore N Bertuccio, Alberto M Martelli, Franco Locatelli, Andrea Pession, Riccardo Masetti