RNA editing for the treatment of alpha-1 antitrypsin deficiency.
RNA 编辑用于治疗 α-1 抗胰蛋白酶缺乏症。
期刊:Nucleic Acids Research
影响因子:13.1
doi:10.1093/nar/gkaf1518
Monian Prashant, Shivalila Chikdu, Lu Genliang, Bowman Keith, Briem Stearne, Bylsma Marissa, Byrne Michael, Cannon Megan, Chatterjee Arindom, Dallaire Morgan, Desai Jigar, Dufresne Jason, Faraone Alyse, Favaloro Frank, Friend Stephen, Ghosh Anamitra, Godfrey Jack, Hernandez Nidia, Huth Olivia, Iwamoto Naoki, Kawamoto Tomomi, Lamattina Anthony, Lemaitre Muriel, Lindsey Amber, Liu Fangjun, Looby Richard, Luu Khoa, McGlynn Andrew, Metterville Jake, Paik Ik-Hyeon, Pan Qianli, Patil Saurabh, Pu Tom, Purcell-Estabrook Erin, Ranade Ashwini, Rheinhardt Jeanette, Rossi Jeff, Shimizu Mamoru, Singh Kuldeep, Standley Stephany, Thomas Carina, Tripathi Snehlata, Yang Hailin, Yordanoff Ryan, Yin Yuan, Yu Hui, Narayanan PadmaKumar, Kandasamy Pachamuthu, Giangrande Paloma H, Vargeese Chandra