日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Assessment of Therapeutic Potential of a Dual AAV Approach for Duchenne Muscular Dystrophy

评估双 AAV 方法治疗杜氏肌营养不良症的潜力

Sonia Albini, Laura Palmieri, Auriane Dubois, Nathalie Bourg, William Lostal, Isabelle Richard

Co-Administration of Simvastatin Does Not Potentiate the Benefit of Gene Therapy in the mdx Mouse Model for Duchenne Muscular Dystrophy

在杜氏肌营养不良症 mdx 小鼠模型中,联合使用辛伐他汀不会增强基因治疗的益处

Nathalie Bourg, Ai Vu Hong, William Lostal, Abbass Jaber, Nicolas Guerchet, Guillaume Tanniou, Fanny Bordier, Emilie Bertil-Froidevaux, Christophe Georger, Nathalie Daniele, Isabelle Richard, David Israeli

Titin M-line insertion sequence 7 is required for proper cardiac function in mice

Titin M 线插入序列 7 是小鼠心脏正常功能所必需的

Ariane Biquand, Simone Spinozzi, Paola Tonino, Jérémie Cosette, Joshua Strom, Zaher Elbeck, Ralph Knöll, Henk Granzier, William Lostal, Isabelle Richard

Single SERCA2a Therapy Ameliorated Dilated Cardiomyopathy for 18 Months in a Mouse Model of Duchenne Muscular Dystrophy

单一 SERCA2a 疗法在杜氏肌营养不良症小鼠模型中改善了扩张型心肌病,持续 18 个月

Nalinda B Wasala, Yongping Yue, William Lostal, Lakmini P Wasala, Nandita Niranjan, Roger J Hajjar, Gopal J Babu, Dongsheng Duan

Titin splicing regulates cardiotoxicity associated with calpain 3 gene therapy for limb-girdle muscular dystrophy type 2A

肌联蛋白剪接调控与2A型肢带型肌营养不良症钙蛋白酶3基因治疗相关的心脏毒性

Lostal, William; Roudaut, Carinne; Faivre, Marine; Charton, Karine; Suel, Laurence; Bourg, Nathalie; Best, Heather; Smith, John Edward; Gohlke, Jochen; Corre, Guillaume; Li, Xidan; Elbeck, Zaher; Knöll, Ralph; Deschamps, Jack-Yves; Granzier, Henk; Richard, Isabelle

Kaposi sarcoma of th e penis in anHIV-negative patient

HIV阴性患者的阴茎卡波西肉瘤

Guevara, José Francisco Aguilar; Fernández, Seila Lacarra; Claros, Oliver Rojas; Villalta, Pedro Giral; Lostal, José Luis Cebrián; Abarzuza, Miguel Angel Resano

Circulating miRNAs are generic and versatile therapeutic monitoring biomarkers in muscular dystrophies

循环miRNA是肌营养不良症中通用且用途广泛的治疗监测生物标志物。

Israeli, David; Poupiot, Jérôme; Amor, Fatima; Charton, Karine; Lostal, William; Jeanson-Leh, Laurence; Richard, Isabelle

A comparison of AAV strategies distinguishes overlapping vectors for efficient systemic delivery of the 6.2 kb Dysferlin coding sequence

AAV 策略比较可区分重叠载体,从而有效地系统性递送 6.2 kb Dysferlin 编码序列

Marina Pryadkina, William Lostal, Nathalie Bourg, Karine Charton, Carinne Roudaut, Matthew L Hirsch, Isabelle Richard

Full-length dystrophin reconstitution with adeno-associated viral vectors

利用腺相关病毒载体进行全长肌营养不良蛋白重建

William Lostal, Kasun Kodippili, Yongping Yue, Dongsheng Duan

Long-term robust myocardial transduction of the dog heart from a peripheral vein by adeno-associated virus serotype-8

通过腺相关病毒8型血清型从外周静脉对犬心脏进行长期、稳定的心肌转导。

Pan, Xiufang; Yue, Yongping; Zhang, Keqing; Lostal, William; Shin, Jin-Hong; Duan, Dongsheng