Etranacogene dezaparvovec in people with hemophilia B with preexisting adeno-associated virus 5 neutralizing antibodies: 4-year subgroup results from the HOPE-B trial
在伴有预先存在的腺相关病毒5型中和抗体的B型血友病患者中应用依曲那康基因(Etranacogene dezaparvovec):HOPE-B试验的4年亚组结果
期刊:Research and Practice in Thrombosis and Haemostasis
影响因子:3.4
doi:10.1016/j.rpth.2026.103360
Klamroth, Robert; Monahan, Paul E; Van der Valk, Paul; Quon, Doris; Kazmi, Rashid Saeed; Coppens, Michiel; O'Connell, Niamh; Pipe, Steven W; von Drygalski, Annette; Afzal, Saira; Gabriel, Richard; Youssar, Loubna; Gill, Sean; Jansen, Nathalie; Wang, Fei; Le Quellec, Sandra; Hermans, Cedric