Human promoter-driven AAV tools enable precision gene therapy targeting cochlear hair cells
人源启动子驱动的腺相关病毒(AAV)工具可实现针对耳蜗毛细胞的精准基因治疗。
期刊:Cell Reports Medicine
影响因子:10.6
doi:10.1016/j.xcrm.2026.102725
Zhang, Liyan; Lu, Yicheng; Wu, Xianmin; Fan, Jinyi; Zhang, Xinru; Xu, Yang; Wei, Hao; Sun, Qiuhan; Jiang, Lulu; Tuo, Huawei; Li, Nianci; Jin, Hua; Cao, Wu; Ye, Beibei; Zhang, Ziyu; Zhang, Yunkai; Chen, Fangyi; Lu, Ling; Qi, Jieyu; Chai, Renjie; Tan, Fangzhi