Universal Prime Editing Therapeutic Strategy for RyR1-Related Myopathies: A Protective Mutation Rescues Leaky RyR1 Channel
针对 RyR1 相关肌病的通用型 Prime 编辑治疗策略:一种保护性突变可挽救 RyR1 通道的渗漏
期刊:International Journal of Molecular Sciences
影响因子:4.9
doi:10.3390/ijms26072835
Godbout, Kelly; Dugas, Mathieu; Reiken, Steven R; Ramezani, Sina; Falle, Alexia; Rousseau, Joël; Wronska, Anetta E; Lamothe, Gabriel; Canet, Geoffrey; Lu, Yaoyao; Planel, Emmanuel; Marks, Andrew R; Tremblay, Jacques P