Early indicators of disease progression in Fabry disease that may indicate the need for disease-specific treatment initiation: findings from the opinion-based PREDICT-FD modified Delphi consensus initiative
法布里病疾病进展的早期指标可能提示需要启动针对特定疾病的治疗:基于意见的PREDICT-FD改良德尔菲共识倡议的研究结果
期刊:BMJ Open
影响因子:2.3
doi:10.1136/bmjopen-2019-035182
Hughes, Derralynn A; Aguiar, Patricio; Deegan, Patrick B; Ezgu, Fatih; Frustaci, Andrea; Lidove, Olivier; Linhart, Aleš; Lubanda, Jean-Claude; Moon, James C; Nicholls, Kathleen; Niu, Dau-Ming; Nowak, Albina; Ramaswami, Uma; Reisin, Ricardo; Rozenfeld, Paula; Schiffmann, Raphael; Svarstad, Einar; Thomas, Mark; Torra, Roser; Vujkovac, Bojan; Warnock, David G; West, Michael L; Johnson, Jack; Rolfe, Mark J; Feriozzi, Sandro