Development and biological characterization of a clinical gene transfer vector for the treatment of MAK-associated retinitis pigmentosa
用于治疗 MAK 相关视网膜色素变性的临床基因转移载体的开发和生物学特性
期刊:Gene Therapy
影响因子:4.6
doi:10.1038/s41434-021-00291-5
Budd A Tucker, Erin R Burnight, Cathryn M Cranston, Mallory J Ulferts, Meagan A Luse, Trudi Westfall, C Anthony Scott, Autumn Marsden, Katherine Gibson-Corley, Luke A Wiley, Ian C Han, Diane C Slusarski, Robert F Mullins, Edwin M Stone