The Global Hypophosphatasia Registry: lessons learned from a decade of real-world data
全球低磷酸酶症登记处:从十年真实世界数据中汲取的经验教训
期刊:Orphanet Journal of Rare Diseases
影响因子:3.5
doi:10.1186/s13023-025-04129-w
Kishnani, Priya S; Seefried, Lothar; Ozono, Keiichi; Martos-Moreno, Gabriel Ángel; Rockman-Greenberg, Cheryl; Fowler, Deborah; Burke, Luke K; Mowrey, William R; Rush, Eric T; Ebeling, Peter R; Högler, Wolfgang; Linglart, Agnès; Fang, Shona; Petryk, Anna; Dahir, Kathryn M