日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Outcomes of Hematopoietic Stem Cell Transplantation in 5 Patients with Autosomal Recessive RIPK1-Deficiency

5例常染色体隐性RIPK1缺陷患者造血干细胞移植的结果

Walsh, Rebecca B; McNaughton, Peter; Nademi, Zohreh; Laberko, Alexandra; Balashov, Dmitry; Al-Mousa, Hamoud; Arkwright, Peter D; Wynn, Robert F; Flood, Terry; Williams, Eleri; Cant, Andrew; Abinun, Mario; Hambleton, Sophie; Slatter, Mary; Gennery, Andrew R; Lum, Su Han; Owens, Stephen

Low rates of endothelial cell dysfunction and transplant-related mortality in 537 children receiving fludarabine-treosulfan conditioning for all transplant indications: A retrospective multicentre study on behalf of the UK Paediatric BMT group

一项由英国儿科骨髓移植组开展的回顾性多中心研究显示,接受氟达拉滨-曲奥舒凡预处理的537名儿童(涵盖所有移植适应症)内皮细胞功能障碍和移植相关死亡率较低。

Altmann, Thomas; Rao, Kanchan; Hanasoge-Nataraj, Ramya; Patrick, Katharine; Carpenter, Ben; Hough, Rachael; Ewins, Anna-Maria; Tewari, Sanjay; Mirci-Danicar, Oana; Slatter, Mary; Wynn, Robert; Lum, Su Han

Personalized hematopoietic stem cell transplantation for inborn errors of immunity

针对先天性免疫缺陷的个性化造血干细胞移植

Slatter, Mary; Lum, Su Han

Hematopoietic Cell Transplantation for Adenosine Deaminase Severe Combined Immunodeficiency-Improved Outcomes in the Modern Era

造血干细胞移植治疗腺苷脱氨酶缺乏症重症联合免疫缺陷——现代医学的疗效提升

Ghimenton, Elisabetta; Flinn, Aisling; Lum, Su Han; Leahy, Timothy R; Nademi, Zohreh; Owens, Stephen; Williams, Eleri; Flood, Terrence; Hambleton, Sophie; Slatter, Mary; Gennery, Andrew R

TCRαβ-Depleted Haploidentical Grafts Are a Safe Alternative to HLA-Matched Unrelated Donor Stem Cell Transplants for Infants with Severe Combined Immunodeficiency

对于患有严重联合免疫缺陷的婴儿,TCRαβ耗竭的单倍体相合移植是HLA匹配的非亲缘供体干细胞移植的一种安全替代方案。

Tsilifis, Christo; Lum, Su Han; Nademi, Zohreh; Hambleton, Sophie; Flood, Terence J; Williams, Eleri J; Owens, Stephen; Abinun, Mario; Cant, Andrew J; Slatter, Mary A; Gennery, Andrew R

Activity of blinatumomab in lymphoblastic leukemia with impaired T-cell immunity due to congenital immunodeficiency

blinatumomab 在先天性免疫缺陷导致 T 细胞免疫受损的淋巴母细胞白血病中的活性

Ramdeny, Sandheeah; Chaudhary, Asima; Worth, Austen; Ghorashian, Sara; Slatter, Mary; Lum, Su Han; Vora, Ajay

Outcome of Hematopoietic Stem Cell Transplantation in patients with Mendelian Susceptibility to Mycobacterial Diseases

孟德尔遗传性分枝杆菌病患者造血干细胞移植的疗效

Radwan, Nesrine; Nademi, Zohreh; Lum, Su Han; Flood, Terry; Abinun, Mario; Owens, Stephen; Williams, Eleri; Gennery, Andrew R; Hambleton, Sophie; Slatter, Mary A

New insights into risk factors for transplant-associated thrombotic microangiopathy in pediatric HSCT

儿童造血干细胞移植相关血栓性微血管病风险因素的新见解

Elfeky, Reem; Lucchini, Giovanna; Lum, Su-Han; Ottaviano, Giorgio; Builes, Natalia; Nademi, Zohreh; Battersby, Alexandra; Flood, Terence; Owens, Stephen; Cant, Andrew J; Young, Helen; Greener, Sinéad; Walsh, Patrick; Kavanagh, David; Annavarapu, Srinivas; Rao, Kanchan; Amrolia, Persis; Chiesa, Robert; Worth, Austen; Booth, Claire; Skinner, Roderick; Doncheva, Bilyana; Standing, Joseph; Gennery, Andrew R; Qasim, Waseem; Slatter, Mary; Veys, Paul

An ICET-A survey on occult and emerging endocrine complications in patients with β-thalassemia major: Conclusions and recommendations

ICET-A关于重型β地中海贫血患者隐匿性和新发内分泌并发症的调查:结论和建议

De Sanctis, Vincenzo; Soliman, Ashraf T; Canatan, Duran; Tzoulis, Ploutarchos; Daar, Shahina; Di Maio, Salvatore; Elsedfy, Heba; Yassin, Mohamed A; Filosa, Aldo; Soliman, Nada; Mehran, Karimi; Saki, Forough; Sobti, Praveen; Kakkar, Shruti; Christou, Soteroula; Albu, Alice; Christodoulides, Constantinos; Kilinc, Yurdanur; Al Jaouni, Soad; Khater, Doaa; Alyaarubi, Saif A; Lum, Su Han; Campisi, Saveria; Anastasi, Salvatore; Galati, Maria Concetta; Raiola, Giuseppe; Wali, Yasser; Elhakim, Ihab Z; Mariannis, Demetris; Ladis, Vassilis; Kattamis, Christos

Prevalence of growth and endocrine disorders in Malaysian children with transfusion-dependent thalassaemia

马来西亚输血依赖型地中海贫血患儿生长发育和内分泌疾病的患病率

Tan, Khian Aun; Lum, Su Han; Yahya, Abqariyah; Krishnan, Shekhar; Jalaludin, Muhammad Yazid; Lee, Way Seah