In vivo prime editing rescues alternating hemiplegia of childhood in mice
体内基因编辑可挽救小鼠儿童交替性偏瘫
期刊:Cell
影响因子:45.5
doi:10.1016/j.cell.2025.06.038.
Alexander A Sousa,Markus Terrey,Holt A Sakai,Christine Q Simmons,Elena Arystarkhova,Natalia S Morsci,Laura C Anderson,Jun Xie,Fabian Suri-Payer,Linda C Laux,Emmanuel Roze,Sylvie Forlani,Guangping Gao,Simon Frost,Nina Frost,Kathleen J Sweadner,Alfred L George Jr,Cathleen M Lutz,David R Liu