Optimizing liver health before and after gene therapy for hemophilia A
血友病A基因治疗前后优化肝脏健康
期刊:Blood Advances
影响因子:7.1
doi:10.1182/bloodadvances.2024013059
Ragni, Margaret V; Mead, Henry; de Jong, Ype P; Kaczmarek, Radoslaw; Leavitt, Andrew D; Long, Brian; Nugent, Diane J; Sabatino, Denise E; Fong, Sylvia; von Drygalski, Annette; Walsh, Christopher E; Luxon, Bruce A