Molecular treatment options for patients carrying KIAA0586/TALPID3 variants.
针对携带 KIAA0586/TALPID3 变异的患者的分子治疗方案
期刊:Molecular Therapy-Nucleic Acids
影响因子:6.1
doi:10.1016/j.omtn.2025.102688
Taudien Jacqueline E, Swirski Sebastian, Möller Maike, Jüschke Christoph, Owczarek-Lipska Marta, Korenke G Christoph, Neidhardt John