AAV9-mediated gene transfer of desmin ameliorates cardiomyopathy in desmin-deficient mice
AAV9 介导的结蛋白基因转移可改善结蛋白缺乏小鼠的心肌病
期刊:Gene Therapy
影响因子:4.6
doi:10.1038/gt.2016.40
M B Heckmann, R Bauer, A Jungmann, L Winter, K Rapti, K-H Strucksberg, C S Clemen, Z Li, R Schröder, H A Katus, O J Müller