Lentivirus-meditated frataxin gene delivery reverses genome instability in Friedreich ataxia patient and mouse model fibroblasts
慢病毒介导的 frataxin 基因传递可逆转弗里德赖希共济失调患者和小鼠模型成纤维细胞中的基因组不稳定性
期刊:Gene Therapy
影响因子:4.6
doi:10.1038/gt.2016.61
H Khonsari, M Schneider, S Al-Mahdawi, Y G Chianea, M Themis, C Parris, M A Pook, M Themis
