Exosomes as nonviral carrier for targeted delivery of CRISPR-Cas12a for therapeutic HIV-1 proviral DNA editing.
外泌体作为非病毒载体,用于靶向递送 CRISPR-Cas12a,以治疗 HIV-1 前病毒 DNA 编辑。
期刊:Molecular Therapy
影响因子:12
doi:10.1016/j.ymthe.2025.11.012
Ma Yan, Wei Wanrong, Yang Zihao, Zhou Ying, Dong Ting, Wang Tao, Xia Xuejiao, Ma Yige, Zhou Mengying, Gao Yang, Yu Boyu, Wang Changjun, Ruan Lianguo, Hong Ke, Gu Chaojiang