Interim results from an ongoing, open-label, single-arm trial of odevixibat in progressive familial intrahepatic cholestasis
正在进行的、开放标签、单臂试验的 odevixibat 治疗进行性家族性肝内胆汁淤积症的中期结果
期刊:Jhep Reports
影响因子:7.5
doi:10.1016/j.jhepr.2023.100782
Thompson, Richard J; Artan, Reha; Baumann, Ulrich; Calvo, Pier Luigi; Czubkowski, Piotr; Dalgic, Buket; D'Antiga, Lorenzo; Di Giorgio, Angelo; Durmaz, Özlem; Gonzalès, Emmanuel; Grammatikopoulos, Tassos; Gupte, Girish; Hardikar, Winita; Houwen, Roderick H J; Kamath, Binita M; Karpen, Saul J; Lacaille, Florence; Lachaux, Alain; Lainka, Elke; Loomes, Kathleen M; Mack, Cara L; Mattsson, Jan P; McKiernan, Patrick; Ni, Quanhong; Özen, Hasan; Rajwal, Sanjay R; Roquelaure, Bertrand; Shteyer, Eyal; Sokal, Etienne; Sokol, Ronald J; Soufi, Nisreen; Sturm, Ekkehard; Tessier, Mary Elizabeth; van der Woerd, Wendy L; Verkade, Henkjan J; Vittorio, Jennifer M; Wallefors, Terese; Warholic, Natalie; Yu, Qifeng; Horn, Patrick; Kjems, Lise