日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Harnessing whole human liver ex situ normothermic perfusion for preclinical AAV vector evaluation

利用全人肝脏离体常温灌注进行临床前 AAV 载体评估

Marti Cabanes-Creus, Sophia H Y Liao, Renina Gale Navarro, Maddison Knight, Deborah Nazareth, Ngee-Soon Lau, Mark Ly, Erhua Zhu, Ramon Roca-Pinilla, Ricardo Bugallo Delgado, Ana F Vicente, Grober Baltazar, Adrian Westhaus, Jessica Merjane, Michael Crawford, Geoffrey W McCaughan, Carmen Unzu, Gloria

Development of CNS tropic AAV1-like variants with reduced liver-targeting following systemic administration in mice

在小鼠体内系统给药后,中枢神经系统嗜性 AAV1 样变体的产生及其肝脏靶向性的降低

Matthieu Drouyer, Jessica Merjane, Deborah Nazareth, Maddison Knight, Suzanne Scott, Sophia H Y Liao, Samantha L Ginn, Erhua Zhu, Ian E Alexander, Leszek Lisowski

AAV capsid bioengineering in primary human retina models

人类视网膜原代模型中的 AAV 衣壳生物工程

Adrian Westhaus, Steven S Eamegdool, Milan Fernando, Paula Fuller-Carter, Alicia A Brunet, Annie L Miller, Rabab Rashwan, Maddison Knight, Maciej Daniszewski, Grace E Lidgerwood, Alice Pébay, Alex Hewitt, Giorgia Santilli, Adrian J Thrasher, Livia S Carvalho, Anai Gonzalez-Cordero, Robyn V Jamieson,

Characterization of the humanized FRG mouse model and development of an AAV-LK03 variant with improved liver lobular biodistribution

人源化 FRG 小鼠模型的表征及具有改善肝小叶生物分布的 AAV-LK03 变体的开发

Marti Cabanes-Creus, Renina Gale Navarro, Sophia H Y Liao, Suzanne Scott, Rodrigo Carlessi, Ramon Roca-Pinilla, Maddison Knight, Grober Baltazar, Erhua Zhu, Matthew Jones, Elena Denisenko, Alistair R R Forrest, Ian E Alexander, Janina E E Tirnitz-Parker, Leszek Lisowski

Development of new adeno-associated virus capsid variants for targeted gene delivery to human cardiomyocytes

开发新型腺相关病毒衣壳变体用于向人类心肌细胞进行靶向基因递送

Cindy Y Kok, Shinya Tsurusaki, Marti Cabanes-Creus, Sindhu Igoor, Renuka Rao, Rhys Skelton, Sophia H Y Liao, Samantha L Ginn, Maddison Knight, Suzanne Scott, Mario Mietzsch, Rebecca Fitzsimmons, Jessica Miller, Tamer M A Mohamed, Robert McKenna, James J H Chong, Adam P Hill, James E Hudson, Ian E Al

High-Throughput In Vitro, Ex Vivo, and In Vivo Screen of Adeno-Associated Virus Vectors Based on Physical and Functional Transduction

基于物理和功能转导的腺相关病毒载体的高通量体外、离体和体内筛选

Adrian Westhaus, Marti Cabanes-Creus, Arkadiusz Rybicki, Grober Baltazar, Renina Gale Navarro, Erhua Zhu, Matthieu Drouyer, Maddison Knight, Razvan F Albu, Boaz H Ng, Predrag Kalajdzic, Magdalena Kwiatek, Kenneth Hsu, Giorgia Santilli, Wendy Gold, Belinda Kramer, Anai Gonzalez-Cordero, Adrian J Thra