Riboflavin transporter deficiency: AAV9-SLC52A2 gene therapy as a new therapeutic strategy.
核黄素转运蛋白缺乏症:AAV9-SLC52A2 基因治疗作为一种新的治疗策略
期刊:Frontiers in Cellular Neuroscience
影响因子:4
doi:10.3389/fncel.2025.1523773
Mei Cecilia, Magliocca Valentina, Chen Xin, Massey Keith, Gonzalez-Cordero Anai, Gray Steven J, Tartaglia Marco, Bertini Enrico Silvio, Corti Stefania, Compagnucci Claudia