Advancing rare disease treatment: EMA's decade-long insights into engineered adoptive cell therapy for rare cancers and orphan designation
推进罕见病治疗:EMA十年来对罕见癌症工程化过继细胞疗法和孤儿药认定的深入研究
期刊:Gene Therapy
影响因子:4.5
doi:10.1038/s41434-024-00446-0
Kalland, Maria Elisabeth; Pose-Boirazian, Tomas; Palomo, Gloria Maria; Naumann-Winter, Frauke; Costa, Enrico; Matusevicius, Darius; Duarte, Dinah M; Malikova, Eva; Vitezic, Dinko; Larsson, Kristina; Magrelli, Armando; Stoyanova-Beninska, Violeta; Mariz, Segundo