日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Efficacy and safety of marstacimab prophylaxis in hemophilia A/B with inhibitors: results from the phase 3 BASIS trial

marstacimab预防治疗A/B型血友病伴抑制剂的疗效和安全性:来自3期BASIS试验的结果

Matino, Davide; Acharya, Suchitra S; Taylor, Carrie Turich; Sun, Pengling; Agathon, Delphine; Raje, Sangeeta; Gould, Travis; Palladino, Andrew; Mahlangu, Johnny; Lissitchkov, Toshko; Todorova, Mariya; Chan, Anthony; Carcao, Manuel; Sun, Jing; Yang, Renchi; Wu, Runhui; Jin, Chenghao; Zeng, Xiaojing; Boban, Ana; Bilic, Ernest; Frenzel, Laurent; Fung Chan, Godfrey Chi; Kong Li, Chi; Apte, Shashikant; Choraria, Nirmalkumar; Chistolini, Antonio; Marchesini, Emanuela; Peyvandi, Flora; Fujii, Teruhisa; Matsushita, Tadashi; Kaneda, Makoto; Lyu, Chuhl Joo; Park, Young Shil; Kim, SungEun; Martinez, Laura Villarreal; Adrian, Javier Morales; Wali, Yasser; Al Khabori, Murtadha; Kurtov, Igor; Alzahrani, Hazzaa; Zaher, Galila; Micic, Dragan; Miljic, Predrag; Kostic, Gordana; Vucic, Miodrag; Djurdjevic, Predrag; Hidalgo, Olga Benitez; Porras, Jose Gonzalez; Jiménez-Yuste, Víctor; Calvo Villas, Jose Manuel; Lopez Fernandez, Maria Fernanda; Albayrak, Canan; Okan, Vahap; Balkan, Can; Sahin, Fahri; Antmen, Ali; Unal, Ekrem; Visweshwar, Nathan; Sharathkumar, Anjali; Kruse-Jarres, Rebecca

Concizumab in hemophilia with inhibitors: longer-term efficacy and safety results from the phase 3 explorer7 study

Concizumab治疗伴有抑制剂的血友病:3期explorer7研究的长期疗效和安全性结果

Mahlangu, Johnny; Boban, Ana; Bruzelius, Maria; Castaman, Giancarlo; Hampton, Kingsley; Knoebl, Paul; Lebreton, Aurélien; Linari, Silvia; López-Jaime, Francisco-José; Martins Mazini Tavares, Camila; Nekkal, Mohamed Salim; Nogami, Keiji; Rhode Høgh Nielsen, Amalie; Shapiro, Amy; d'Oiron, Roseline

Durability of efficacy, safety, and quality of life 5 years after valoctocogene roxaparvovec gene transfer for severe hemophilia A: final phase 3 GENEr8-1 trial results

接受valoctocogene roxaparvovec基因转移治疗重度A型血友病5年后,疗效、安全性和生活质量的持久性:GENEr8-1 III期临床试验的最终结果

Leavitt, Andrew D; Mahlangu, Johnny; Raheja, Priyanka; Symington, Emily; Quon, Doris V; Giermasz, Adam; Kenet, Gili; Lowe, Gillian; Key, Nigel S; Millar, Carolyn M; Pipe, Steven W; Chou, Sheng-Chieh; Klamroth, Robert; Mason, Jane; Chambost, Hervé; Peyvandi, Flora; Majerus, Elaine; Pepperell, Dominic; Tan, Chee Wee; Yu, Hua; Chavele, Konstantia-Maria; Ozelo, Margareth C

Sustained Clinical Benefit of AAV Gene Therapy in Severe Hemophilia B

AAV基因疗法在重度B型血友病中持续发挥临床疗效

Reiss, Ulrike M; Davidoff, Andrew M; Tuddenham, Edward G D; Chowdary, Pratima; McIntosh, Jenny; Muczynski, Vincent; Journou, Malo; Simini, Giulia; Ireland, Lydia; Mohamed, Saira; Riddell, Anne; Pie, Arnulfo J; Hall, Andrew; Quaglia, Alberto; Mangles, Sarah; Mahlangu, Johnny; Haley, Kristina; Recht, Michael; Shen, Yu-Min; Halka, Kathleen G; Fortner, Gail; Morton, Christopher L; Gu, Zhengming; Hayden, Randall T; Neufeld, Ellis J; Okhomina, Victoria I; Kang, Guolian; Nathwani, Amit C

Marstacimab prophylaxis in hemophilia A/B without inhibitors: results from the phase 3 BASIS trial

在无抑制剂的A/B型血友病患者中应用马斯替单抗进行预防性治疗:来自3期BASIS试验的结果

Matino, Davide; Palladino, Andrew; Taylor, Carrie Turich; Hwang, Eunhee; Raje, Sangeeta; Nayak, Satyaprakash; McDonald, Regina; Acharya, Suchitra S; Mahlangu, Johnny; Jiménez-Yuste, Victor; Choraria, Nirmalkumar; Yang, Renchi; Li, Chi-Kong; Al-Khabori, Murtadha; Wali, Yasser; Morales Adrián, Javier; Park, Young-Shil; Zülfikar, O Bülent; Teeter, John

Haemophilia and access to gene therapy

血友病与基因治疗的可及性

Mahlangu, Johnny

Guidelines for management of hemophilia-why, what, and how?

血友病管理指南——为什么、做什么以及如何做?

Srivastava, Alok; Mahlangu, Johnny; Pipe, Steven W

Adeno-associated virus-based gene therapy for hemophilia-addressing the gaps

腺相关病毒介导的血友病基因治疗——弥补现有差距

Miesbach, Wolfgang; Batty, Paul; Chowdary, Pratima; Fong, Sylvia; Kaczmarek, Radoslaw; Leebeek, Frank W G; Long, Brian; Mahlangu, Johnny; Makris, Mike; Pierce, Glenn F; Pipe, Steven W; Srivastava, Alok; Voorberg, Jan; Peyvandi, Flora

FRONTIER1 multiple ascending dose extension: a safety, tolerability, pharmacokinetics, and pharmacodynamics study of Mim8 in people with hemophilia A

FRONTIER1 多次递增剂量扩展研究:一项针对 A 型血友病患者的 Mim8 安全性、耐受性、药代动力学和药效学研究

Chowdary, Pratima; Lentz, Steven R; Gil, Lidia; López-Jaime, Francisco J; Windyga, Jerzy; Ong Clausen, Wan Hui; Laursen, Peter Nørkjær; Mahlangu, Johnny

Trenonacog alfa safety, efficacy, and pharmacokinetics in previously treated pediatric hemophilia B

Trenonacog alfa 在既往接受过治疗的儿童血友病 B 患者中的安全性、有效性和药代动力学研究

Vilchevska, Kateryna; Balkan, Can; Turea, Valentin; Gurtchumelia, Darejani; Loureiro Prezotti, Alessandra Nunes; Oliveira de Oliveira, Luciana Correa; Leon, Julissa; Fosdal, Mark; Mahlangu, Johnny