Safety and effectiveness of ataluren in patients with Duchenne muscular dystrophy: single-center experience from Saudi Arabia
阿塔卢伦治疗杜氏肌营养不良症患者的安全性和有效性:沙特阿拉伯单中心经验
期刊:Journal of International Medical Research
影响因子:1.5
doi:10.1177/03000605241305252
Ahmad, Mushtaha; ElRasoul, Alaa; Sedayou, Raneem; Tamboosi, Mohammed; Mahroos, Hanan; Alrashed, Shaimaa; Tunkar, Mariam; Alzahrani, Faisal; Alharbi, Mohammed; Aljehani, Mona; Alahmari, Mousa; Alqarni, Khalid; Gashlan, Maha; Yilmaz, Berna Seker; Alshaikh, Nahla M