日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

STARR-CRAAVT: A platform to identify cell type-specific regulatory elements for next-generation gene therapy

STARR-CRAAVT:用于识别下一代基因治疗的细胞类型特异性调控元件的平台

Becker, Robert; Choudhury, Priyanka; Oti, Martin; Fouani, Youssef; Strobel, Benjamin; Ketterer, Stephanie; Rumpel, Simon; Park, John; Kreuz, Sebastian; Maier, Udo; Michelfelder, Stefan; Schön, Christian

Pharmacological and pre-clinical safety profile of rSIV.F/HN, a hybrid lentiviral vector for cystic fibrosis gene therapy

rSIV.F/HN(一种用于囊性纤维化基因治疗的混合慢病毒载体)的药理学和临床前安全性概况

Moiseenko, Alena; Sinadinos, Anthony; Sergijenko, Ana; Pineault, Kyriel; Saleh, Aarash; Nekola, Konradin; Strang, Nathalie; Eleftheraki, Anastasia; Boyd, A Christopher; Davies, Jane C; Gill, Deborah R; Hyde, Stephen C; McLachlan, Gerry; Rath, Tim; Rothe, Michael; Schambach, Axel; Hobbie, Silke; Schuler, Michael; Maier, Udo; Thomas, Matthew J; Mennerich, Detlev; Schmidt, Manfred; Griesenbach, Uta; Alton, Eric W F W; Kreuz, Sebastian

3D co-cultures of primary human hepatocytes and Kupffer-like cells to address innate immune responses to rAAV.

利用原代人肝细胞和库普弗样细胞的 3D 共培养来研究对 rAAV 的先天免疫反应。

Ramella Gal Isabella, Arez Francisca, Correia Inês P, Domenici Giacomo, Fernandes Sofia, Silva Gabriela, Saldanha Inês, Duarte Nadia, Freitas Catarina, Alves Paula M, Maier Udo, Coroadinha Ana Sofia, du Plessis François, Brito Catarina

αFAP-specific nanobodies mediate a highly precise retargeting of modified AAV2 capsids thereby enabling specific transduction of tumor tissues.

αFAP 特异性纳米抗体介导对修饰的 AAV2 衣壳进行高度精确的重新靶向,从而实现对肿瘤组织的特异性转导

Olarewaju Olaniyi, Held Franziska, Curtis Pamela, Kenny Cynthia Hess, Maier Udo, Panavas Tadas, du Plessis Francois