Efficient and safe therapeutic use of paired Cas9-nickases for primary hyperoxaluria type 1
高效安全地利用成对Cas9切口酶治疗原发性高草酸尿症1型
期刊:EMBO Molecular Medicine
影响因子:9
doi:10.1038/s44321-023-00008-8
Laura Torella,Julia Klermund #,Martin Bilbao-Arribas #,Ibon Tamayo,Geoffroy Andrieux,Kay O Chmielewski,Africa Vales,Cristina Olagüe,Daniel Moreno-Luqui,Ivan Raimondi,Amaya Abad,Julen Torrens-Baile,Eduardo Salido,Maite Huarte,Mikel Hernaez,Melanie Boerries,Toni Cathomen #,Nerea Zabaleta #,Gloria Gonzalez-Aseguinolaza #