日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Exploring Affordable Curative Therapy for Sickle Cell Disease in Africa: A Comprehensive Overview

探索非洲镰状细胞病的经济有效疗法:一项综合概述

Kassim, Adetola A; Thompson, Alexis A; Malik, Punam

Lentiviral gene therapy with reduced-intensity conditioning for sickle cell disease: a phase 1/2 trial

采用减低强度预处理的慢病毒基因疗法治疗镰状细胞病:一项 1/2 期试验

Grimley, Michael; Davies, Stella M; Shrestha, Archana; Shova, Amy; Asnani, Monika; Kent, Michael; Sayani, Farzana; Quinn, Charles T; Niss, Omar; Lutzko, Carolyn; Mehta, Parinda A; Khandelwal, Pooja; Little, Courtney; Chandra, Sharat; Felker, Sydney; Chi, Mengna; Kalfa, Theodosia A; Knight-Madden, Jennifer; Arumugam, Paritha I; Ramos, Kristie N; Witting, Scott; Latham, Teresa; Bushman, Frederic D; Malik, Punam

A novel mouse model of hemoglobin SC disease reveals mechanisms underlying beneficial effects of hydroxyurea

一种新型的血红蛋白SC疾病小鼠模型揭示了羟基脲发挥有益作用的潜在机制

Setayesh, Tahereh; Chi, Mengna; Oestreicher, Zachery; Sakabe, Masahide; Seu, Katie; Zhu, Zhenqi; Kaur, Harsimran; Tijani, Anifat; Xin, Mei; Shova, Amy; Greis, Kenneth D; Townes, Tim M; Balla, József; VandenHeuvel, Katherine; Hu, Yueh-Chiang; Malik, Punam

An engineered β-globin homology donor reveals insights into β-globin expression and betters HDR

工程化β-珠蛋白同源供体揭示了β-珠蛋白表达的奥秘,并改善了HDR。

Chi, Mengna; Malik, Punam

Preclinical efficacy of a modified gamma-globin lentivirus gene therapy in Berkeley sickle cell anemia mice and human xenograft models.

改良型γ-珠蛋白慢病毒基因疗法在伯克利镰状细胞贫血小鼠和人类异种移植模型中的临床前疗效。

Shrestha Archana, Pillis Devin M, Felker Sydney, Chi Mengna, Wagner Kimberly, Gbotosho Oluwabukola T, Sieling Joseph, Shadid Mohammad, Malik Punam

Longitudinal changes and predictors of cardiac extracellular volume fraction in sickle cell anemia

镰状细胞贫血症患者心脏细胞外容积分数的纵向变化及预测因素

Niss, Omar; Morin, Cara E; Hashemi, Sassan; Alsaied, Tarek; Lang, Sean M; Taylor, Michael D; Tasset, MacKenzie; Malik, Punam; Quinn, Charles T

HGG-07. INVESTIGATING THE ROLE OF SENESCENCE IN PEDIATRIC HIGH-GRADE GLIOMAS

HGG-07. 研究衰老在儿童高级别胶质瘤中的作用

Arumugam, Paritha I; Higashimoto, Tomoyasu; Urbinati, Fabrizia; Modlich, Ute; Nestheide, Shawna; Xia, Ping; Fox, Catherine; Corsinotti, Andrea; Baum, Christopher; Malik, Punam; Chang, Timothy H; Nassar, Alexander; Kleinman, Claudia; Bandopadhayay, Pratiti

NRAS(Q61R) mutation drives elevated angiopoietin-2 expression in human endothelial cells and a genetic mouse model.

NRAS(Q61R)突变驱动人类内皮细胞和基因小鼠模型中血管生成素-2表达升高

Pastura Patricia, McDaniel C Griffin, Alharbi Sara, Fox Dermot, Coleman Bethany, Malik Punam, Adams Denise M, Le Cras Timothy D

Strategies for precise gene edits in mammalian cells

哺乳动物细胞精确基因编辑策略

Fichter, Katye M; Setayesh, Tahereh; Malik, Punam

Correction: Towards access for all: 1st Working Group Report for the Global Gene Therapy Initiative (GGTI)

更正:迈向人人享有基因治疗:全球基因治疗倡议(GGTI)第一工作组报告

Adair, Jennifer E; Androski, Lindsay; Bayigga, Lois; Bazira, Deus; Brandon, Eugene; Dee, Lynda; Deeks, Steven; Draz, Mohamed; Dubé, Karine; Dybul, Mark; Gurkan, Umut; Harlow, Evelyn; Kityo, Cissy; Louella, Michael; Malik, Punam; Mathews, Vikram; McKemey, Adrian; Mugerwa, Henry; Muyanja, Daniel; Olayiwola, Olabimpe; Orentas, Rimas J; Popovski, Alex; Sheehy, Jeff; Ssali, Francis; Nsubuga, Moses Supercharger; Tisdale, John F; Verhoeyen, Els; Dropulić, Boro