Exploring exon excision as a therapeutic intervention strategy for the future treatment of ADGRV1-associated retinitis pigmentosa
探索外显子切除作为未来治疗ADGRV1相关性视网膜色素变性的治疗干预策略
期刊:Molecular Therapy-Nucleic Acids
影响因子:6.1
doi:10.1016/j.omtn.2025.102702
Stemerdink, Merel; Malinar, Lucija; Broekman, Sanne; Peters, Theo; Ensink, Iris; Ivanchenko, Maryna V; Venselaar, Hanka; Kremer, Hannie; de Vrieze, Erik; van Wijk, Erwin