Comparative evaluation of liver-directed knockin strategies with viral and nonviral vectors in mouse inherited disease models.
在小鼠遗传疾病模型中,对以病毒载体和非病毒载体为靶点的肝脏基因敲入策略进行比较评价。
期刊:Molecular Therapy
影响因子:12
doi:10.1016/j.ymthe.2025.12.012
Jin Xiu, Wu Xiaoyi, Song Junwei, Luo Mei, Ye Qin, Ren Chengda, Song Li, Li Manjun, Hu Ming, An Yifang, Su Jing, Fu Jiamei, Xu Qiuxia, Luo Min, Liu Fanfei, Liu Man, Li Qiqi, Yao Shaohua, Chen Lu, Yang Yang