日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Defining RNA oligonucleotides that reverse deleterious phase transitions of RNA-binding proteins with prion-like domains.

确定能够逆转具有朊病毒样结构域的 RNA 结合蛋白的有害相变的 RNA 寡核苷酸。

Guo Lin, Mann Jacob R, Mauna Jocelyn C, Copley Katie E, Wang Hejia, Rubien Jack D, Bergmann Cristian A, Carey Jenny L, Merjane Jessica, Ngo Marilyn, Xu Jiazhen, Odeh Hana M, Lin JiaBei, Lee Bo Lim, Ganser Laura, Robinson Emma, Kim Kevin M, Murthy Anastasia C, Paul Tapas, Portz Bede, Gleixner Amanda M, Diaz Zamia, Smirnov Ashleigh, Padilla George, Lavorando Ellen, Espy Carolann, Shang Yulei, Huang Eric J, Chesi Alessandra, Fawzi Nicolas L, Myong Sua, Donnelly Christopher J, Shorter James

TDP-43-dependent mis-splicing of KCNQ2 triggers intrinsic neuronal hyperexcitability in ALS/FTD.

TDP-43 依赖的 KCNQ2 错误剪接引发 ALS/FTD 中的内在神经元过度兴奋。

Joseph Brian J, Marshall Kelly A, Harley Peter, Mann Jacob R, Alessandrini Francesco, Vanoye Carlos G, Chi Wanhao, Prudencio Mercedes, Simkin Dina, Kao Tzu-Ting, Desai Reshma R, Keuss Matthew J, Barattucci Simone, Zanovello Matteo, Mehta Puja R, DeKeyser Jean-Marc, Limone Francesco, Lee Jonathan, Brown Anna-Leigh, Leyton-Jaimes Marcel F, Nash Leslie A, Juan Irune Guerra San, Aronica Eleonora, Wainger Brian J, Shah Mala, Goswami Anand, Shneider Neil A, Dickson Dennis W, Burrone Juan, Zhang Chaolin, Wichterle Hynek, Petrucelli Leonard, Watts Jonathan K, George Alfred L Jr, Fratta Pietro, Eggan Kevin, Kiskinis Evangelos

Defining RNA oligonucleotides that reverse deleterious phase transitions of RNA-binding proteins with prion-like domains

确定能够逆转具有朊病毒样结构域的RNA结合蛋白的有害相变的RNA寡核苷酸

Guo, Lin; Mann, Jacob R; Mauna, Jocelyn C; Copley, Katie E; Wang, Hejia; Rubien, Jack D; Odeh, Hana M; Lin, JiaBei; Lee, Bo Lim; Ganser, Laura; Robinson, Emma; Kim, Kevin M; Murthy, Anastasia C; Paul, Tapas; Portz, Bede; Gleixner, Amanda M; Diaz, Zamia; Carey, Jenny L; Smirnov, Ashleigh; Padilla, George; Lavorando, Ellen; Espy, Carolann; Shang, Yulei; Huang, Eric J; Chesi, Alessandra; Fawzi, Nicolas L; Myong, Sua; Donnelly, Christopher J; Shorter, James

RNA modulates physiological and neuropathological protein phase transitions

RNA调节生理和神经病理学中的蛋白质相变

Mann, Jacob R; Donnelly, Christopher J

Optogenetic TDP-43 nucleation induces persistent insoluble species and progressive motor dysfunction in vivo.

光遗传学 TDP-43 成核作用可诱导体内持续存在的不溶性物质和进行性运动功能障碍

Otte Charlton G, Fortuna Tyler R, Mann Jacob R, Gleixner Amanda M, Ramesh Nandini, Pyles Noah J, Pandey Udai B, Donnelly Christopher J

Hypoxic-Preconditioned Bone Marrow Stem Cell Medium Significantly Improves Outcome After Retinal Ischemia in Rats.

缺氧预处理的骨髓干细胞培养基显著改善了大鼠视网膜缺血后的预后

Roth Steven, Dreixler John C, Mathew Biji, Balyasnikova Irina, Mann Jacob R, Boddapati Venkat, Xue Lai, Lesniak Maciej S