Pharmacodynamics, safety, tolerability and pharmacokinetics of a single oral dose of an engineered phenylalanine ammonia-lyase in patients with phenylketonuria
苯丙酮尿症患者单次口服工程化苯丙氨酸解氨酶的药效学、安全性、耐受性和药代动力学研究
期刊:Molecular Genetics and Metabolism Reports
影响因子:1.9
doi:10.1016/j.ymgmr.2023.101012
Fazio, Timothy Nicholas; Healy, Louise; Heise, Tim; Inwood, Anita; Manolikos, Catherine; Rahman, Yusof; Woerle, Hans-Juergen; Hendriksz, Christian J
