日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Trans-splicing into highly abundant albumin transcripts for production of therapeutic proteins in vivo.

反式剪接形成高丰度白蛋白转录本,用于在体内生产治疗性蛋白质

Wang Jun, Mansfield S Gary, Cote Colette A, Jiang Ping Du, Weng Ke, Amar Marcelo J A, Brewer Bryan H Jr, Remaley Alan T, McGarrity Gerard J, Garcia-Blanco Mariano A, Puttaraju M

Correction of tau mis-splicing caused by FTDP-17 MAPT mutations by spliceosome-mediated RNA trans-splicing

通过剪接体介导的RNA反式剪接纠正FTDP-17 MAPT突变引起的tau蛋白错误剪接

Rodriguez-Martin, Teresa; Anthony, Karen; Garcia-Blanco, Mariano A; Mansfield, S Gary; Anderton, Brian H; Gallo, Jean-Marc