日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Ultrasound-mediated gene delivery specifically targets liver sinusoidal endothelial cells for sustained FVIII expression in hemophilia A mice.

超声介导的基因递送可特异性地靶向肝窦内皮细胞,从而在 A 型血友病小鼠中实现持续的 FVIII 表达

Lawton Savannah M, Manson Megan A, Fan Meng-Ni, Chao Ting-Yen, Chen Chun-Yu, Kim Peter, Campbell Carley, Cai Xiaohe, Vander Kooi Amber, Miao Carol H

Transcutaneous ultrasound-mediated gene delivery into canine livers achieves therapeutic levels of factor VIII expression

经皮超声介导的基因递送至犬肝脏可达到治疗水平的VIII因子表达。

Manson, Megan A; Zhang, Feng; Novokhodko, Alexander; Chen, Chun-Yu; Parker, Maura; Loeb, Keith R; Kajimoto, Masaki; Campbell, Carley; Storb, Rainer F; Miao, Carol H

Human retinal pigment epithelial cells prefer proline as a nutrient and transport metabolic intermediates to the retinal side

人类视网膜色素上皮细胞偏好脯氨酸作为营养物质,并将代谢中间体运输到视网膜侧。

Chao, Jennifer R; Knight, Kaitlen; Engel, Abbi L; Jankowski, Connor; Wang, Yekai; Manson, Megan A; Gu, Haiwei; Djukovic, Danijel; Raftery, Daniel; Hurley, James B; Du, Jianhai