Rationale and design of MUSIC-HFpEF: a phase 1b, pilot trial evaluating the safety and pharmacodynamic effects of AAV1.SERCA2A in heart failure with preserved ejection fraction
MUSIC-HFpEF 研究的原理和设计:一项 1b 期试点试验,旨在评估 AAV1.SERCA2A 在射血分数保留型心力衰竭中的安全性和药效学作用。
期刊:Heart Failure Reviews
影响因子:4.2
doi:10.1007/s10741-025-10589-w
Fudim, Marat; Sarma, Satyam; MacNamara, James P; Ascheim, Deborah D; Kittipibul, Veraprapas; Doukellis, Katheryn; Dhimitri, Andy; Fitzhugh, Robert; Kamat, Niharika; Costa, Kevin D; Rudy, Jeffrey; Guerrero, Janet; Chan, Camie; Li, Ronald A; Bavry, Anthony A; Patel, Manesh R; Grodin, Justin L; Levine, Benjamin D; Hajjar, Roger J