日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Improved efficacy of FKRP AAV gene therapy by combination with ribitol treatment for LGMD2I

FKRP AAV 基因治疗联合核糖醇治疗 LGMD2I 疗效提高

Marcela P Cataldi, Charles H Vannoy, Anthony Blaeser, Jason D Tucker, Victoria Leroy, Raegan Rawls, Jessalyn Killilee, Molly C Holbrook, Qi Long Lu

ISPD Overexpression Enhances Ribitol-Induced Glycosylation of α-Dystroglycan in Dystrophic FKRP Mutant Mice

ISPD 过表达增强营养不良 FKRP 突变小鼠中核糖醇诱导的 α-Dystroglycan 糖基化

Marcela P Cataldi, Anthony Blaeser, Peijuan Lu, Victoria Leroy, Qi Long Lu

Ribitol restores functionally glycosylated α-dystroglycan and improves muscle function in dystrophic FKRP-mutant mice

利比醇可恢复功能性糖基化 α-肌营养不良症聚糖并改善营养不良症 FKRP 突变小鼠的肌肉功能

Marcela P Cataldi, Peijuan Lu, Anthony Blaeser, Qi Long Lu

Differential effects of DNA double-strand break repair pathways on single-strand and self-complementary adeno-associated virus vector genomes

DNA双链断裂修复途径对单链和自互补腺相关病毒载体基因组的不同影响

Marcela P Cataldi, Douglas M McCarty