日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Aiolos and Eos drive distinct human TH17 functional states

Aiolos 和 Eos 驱动不同的人类 TH17 功能状态

Cerboni, Silvia; Mohammadnezhad, Leila; Agrawal, Komal; Budida, Ramachandramouli; Papa, Ilenia; Gaggero, Silvia; Dulong, Joel; Cole, Anna; Mezger, Anja; Yan, Bingyu; Zhang, Zonghao; Israelsson, Elisabeth; Volkov, Petr; Li, Songyuan; Caceres, Eva F; Leprohon, Malo; Azgomi, Mojtaba Shekarkar; Cui, Yue; Salemio, Svitlana; Firth, Mike; Wigge, Leif; Rudin, Anna; Grindebacke, Hanna; Maresca, Marcello; Paulos, Chrystal; Morschhauser, Franck; Manier, Salomon; Kazemian, Majid; Laurence, Arian; Hühn, Michael; Gehrmann, Ulf; Tarte, Karin; Mitra, Suman

A prime editing strategy to rewrite the γ-globin promoters and reactivate fetal hemoglobin for sickle cell disease

镰状细胞病的主要编辑策略是重写γ-珠蛋白启动子并重新激活胎儿血红蛋白。

Chalumeau, Anne; Bou Dames, Maria; Fontana, Letizia; Amistadi, Simone; Antoniou, Panagiotis; Loganathan, Priyanka; Mombled, Margaux; Corre, Guillaume; Peterka, Martin; Amendola, Mario; Giovannangeli, Carine; Maresca, Marcello; Miccio, Annarita; Brusson, Mégane

Dual inhibition of DNA-PK and PolÏ´ boosts precision of diverse prime editing systems.

DNA-PK 和 PolÏ´ 的双重抑制提高了各种主要编辑系统的精确度

Dacquay Louis C, Antoniou Panagiotis, Mentani Astrid, Selfjord Niklas, MÃ¥rtensson Hanna, Hsieh Pei-Pei, Mustfa Salman, Thom George, Wimberger Sandra, Firth Mike, Akrap Nina, Maresca Marcello, Peterka Martin

Prime Editing: Mechanistic Insights and DNA Repair Modulation

主编辑:机制见解和DNA修复调控

Mentani, Astrid; Maresca, Marcello; Shiriaeva, Anna

Engineered PsCas9 enables therapeutic genome editing in mouse liver with lipid nanoparticles

利用脂质纳米颗粒对小鼠肝脏进行基因工程改造的PsCas9基因编辑,可实现治疗性基因组编辑。

Degtev, Dmitrii; Bravo, Jack; Emmanouilidi, Aikaterini; Zdravković, Aleksandar; Choong, Oi Kuan; Liz Touza, Julia; Selfjord, Niklas; Weisheit, Isabel; Francescatto, Margherita; Akcakaya, Pinar; Porritt, Michelle; Maresca, Marcello; Taylor, David; Sienski, Grzegorz

Progress and harmonization of gene editing to treat human diseases: Proceeding of COST Action CA21113 GenE-HumDi

基因编辑治疗人类疾病的进展与协调:COST行动CA21113 GenE-HumDi会议记录

Cavazza, Alessia; Hendel, Ayal; Bak, Rasmus O; Rio, Paula; Güell, Marc; Lainšček, Duško; Arechavala-Gomeza, Virginia; Peng, Ling; Hapil, Fatma Zehra; Harvey, Joshua; Ortega, Francisco G; Gonzalez-Martinez, Coral; Lederer, Carsten W; Mikkelsen, Kasper; Gasiunas, Giedrius; Kalter, Nechama; Gonçalves, Manuel A F V; Petersen, Julie; Garanto, Alejandro; Montoliu, Lluis; Maresca, Marcello; Seemann, Stefan E; Gorodkin, Jan; Mazini, Loubna; Sanchez, Rosario; Rodriguez-Madoz, Juan R; Maldonado-Pérez, Noelia; Laura, Torella; Schmueck-Henneresse, Michael; Maccalli, Cristina; Grünewald, Julian; Carmona, Gloria; Kachamakova-Trojanowska, Neli; Miccio, Annarita; Martin, Francisco; Turchiano, Giandomenico; Cathomen, Toni; Luo, Yonglun; Tsai, Shengdar Q; Benabdellah, Karim

Harnessing DSB repair to promote efficient homology-dependent and -independent prime editing

利用DSB修复促进高效的同源依赖性和非同源性起始编辑

Peterka, Martin; Akrap, Nina; Li, Songyuan; Wimberger, Sandra; Hsieh, Pei-Pei; Degtev, Dmitrii; Bestas, Burcu; Barr, Jack; van de Plassche, Stijn; Mendoza-Garcia, Patricia; Šviković, Saša; Sienski, Grzegorz; Firth, Mike; Maresca, Marcello

Improving Precise CRISPR Genome Editing by Small Molecules: Is there a Magic Potion?

利用小分子提高 CRISPR 基因组编辑的精确度:是否存在灵丹妙药?

Bischoff, Nadja; Wimberger, Sandra; Maresca, Marcello; Brakebusch, Cord

Unbiased detection of CRISPR off-targets in vivo using DISCOVER-Seq

利用 DISCOVER-Seq 技术在体内进行无偏 CRISPR 脱靶效应检测

Wienert, Beeke; Wyman, Stacia K; Richardson, Christopher D; Yeh, Charles D; Akcakaya, Pinar; Porritt, Michelle J; Morlock, Michaela; Vu, Jonathan T; Kazane, Katelynn R; Watry, Hannah L; Judge, Luke M; Conklin, Bruce R; Maresca, Marcello; Corn, Jacob E

Decoding non-random mutational signatures at Cas9 targeted sites.

解码 Cas9 靶位点的非随机突变特征

Taheri-Ghahfarokhi Amir, Taylor Benjamin J M, Nitsch Roberto, Lundin Anders, Cavallo Anna-Lina, Madeyski-Bengtson Katja, Karlsson Fredrik, Clausen Maryam, Hicks Ryan, Mayr Lorenz M, Bohlooly-Y Mohammad, Maresca Marcello